Quality of life and unmet needs in patients with fabry disease: a qualitative study

Abstract Background Patients with Fabry disease (FD) consider their quality of life to be significantly affected. The majority of studies evaluate the quality of life using quantitative measures and standardised scales that offer relevant information about experience with the disease in multiple asp...

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Bibliographic Details
Main Authors: Montserrat Morales, Jordi Cruz, Eduardo Brignani, Laura Acuña, Esther Lázaro, Cristina Soria
Format: Article
Language:English
Published: BMC 2024-10-01
Series:Orphanet Journal of Rare Diseases
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Online Access:https://doi.org/10.1186/s13023-024-03412-6
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