Importance of Long-Term Follow-Up in the Prognosis of Mucopolysaccharidosis IV-A: A Case Report from Southwestern of Colombia

Abstract Mucopolysaccharidosis IV-A (MPS IV-A) is an autosomal recessive genetic disorder caused by a deficiency in the enzyme N-acetylgalactosamine-6-sulfatase, leading to the accumulation of chondroitin-6-sulfate (C6S) and keratan sulfate (KS). This is a rare disease, and, in Colombia, it is class...

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Bibliographic Details
Main Authors: Mariana Ardila Marín, Carlos Arturo Caicedo Toro, Jeyson Steven Rojas Banguero, José María Satizabal Soto, Daniela Arturo Terranova
Format: Article
Language:English
Published: SciELO 2025-06-01
Series:Journal of Inborn Errors of Metabolism and Screening
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Online Access:http://www.scielo.br/scielo.php?script=sci_arttext&pid=S2326-45942025000100602&lng=en&tlng=en
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