How a patient-led advocacy organization supports the road to diagnosis and treatment of creatine transporter deficiency

The current era of drug development has evolved significantly. Patient advocacy organizations are moving beyond simply supporting community members and are taking the reins to improve the speed of diagnoses, initiate therapeutic discoveries, and lay the groundwork to ensure successful clinical trial...

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Bibliographic Details
Main Authors: Heidi Wallis, Sangeetha Iyer, Emily K. Reinhardt
Format: Article
Language:English
Published: Frontiers Media S.A. 2025-02-01
Series:Frontiers in Neuroscience
Subjects:
Online Access:https://www.frontiersin.org/articles/10.3389/fnins.2025.1548182/full
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