Porcupine inhibition is a promising pharmacological treatment for severe sclerosteosis pathologies

Abstract Sclerosteosis, an ultra-rare disorder characterised by high bone mass (HBM) and skeletal overgrowth, leads to facial paralysis, hearing loss and raised intracranial pressure, which is currently managed only through high-risk surgery. Sclerosteosis is caused by SOST mutations and loss of fun...

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Bibliographic Details
Main Authors: Timothy J. Dreyer, Jacob A. C. Keen, Leah M. Wells, Mark Hopkinson, Isabel R. Orriss, Gill Holdsworth, Andrew A. Pitsillides, Scott J. Roberts
Format: Article
Language:English
Published: Nature Publishing Group 2025-04-01
Series:Bone Research
Online Access:https://doi.org/10.1038/s41413-025-00406-3
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