Myopathy, lactic acidosis and sideroblastic anemia syndrome 1 (MLASA1): clinical hallmarks in a large pedigree with a novel <i>PUS1</i> R144Q mutation, remarkable response to somatropin, and review of the literature

Not available.

Saved in:
Bibliographic Details
Main Authors: Lorenzo Parisi, Robert Escher
Format: Article
Language:English
Published: Ferrata Storti Foundation 2025-05-01
Series:Haematologica
Online Access:https://haematologica.org/article/view/12081
Tags: Add Tag
No Tags, Be the first to tag this record!