P070: Follow-up of very attenuated form of mucopolysaccharidosis type Ⅱ detected by newborn screening

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Bibliographic Details
Main Authors: Yuta Sudo, Yoko Nakajima, Yasuaki Yasuda, Tetsushi Yoshikawa, Tetsuya Ito
Format: Article
Language:English
Published: Elsevier 2025-01-01
Series:Genetics in Medicine Open
Online Access:http://www.sciencedirect.com/science/article/pii/S2949774425009537
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