miR-33 inhibition as a novel therapeutic approach for treating muscular dystrophy

Duchenne muscular dystrophy (DMD) is a devastating disorder caused by pathogenic variants in the dystrophin gene resulting in the absence of a functional dystrophin protein. While the primary cause of DMD is well-documented, the impact of disrupted secondary signaling pathways in dystrophic muscles...

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Bibliographic Details
Main Authors: Michael A Lopez, Matthew S Alexander
Format: Article
Language:English
Published: Springer Nature 2025-07-01
Series:EMBO Molecular Medicine
Online Access:https://doi.org/10.1038/s44321-025-00271-x
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