Real-world tafamidis experience in hereditary transthyretin amyloidosis with peripheral neuropathy in Brazil

Real-world tafamidis experience in hereditary transthyretin amyloidosis with peripheral neuropathy in Brazil

Background Tafamidis is a kinetic stabilizer that binds to the transthyretin (TTR) gene, inhibiting its dissociation. It is the only disease-modifying treatment for hereditary TTR amyloidosis with peripheral neuropathy (ATTRv-PN) available in the National Therapeutic Form (Formulário Tera...

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Main Authors: Luiz Felipe Pinto, Marcus V. Pinto, Paula Accioli, Gabriela Amorim, Renata Gervais de Santa Rosa, Moises Dias, Mariana Guedes, Carlos P. Gomez, Roberto C. Pedrosa, Marcia Waddington-Cruz
Format: Article
Language:English
Published: Academia Brasileira de Neurologia (ABNEURO) 2025-01-01
Series:Arquivos de Neuro-Psiquiatria
Subjects:
Polyneuropathies
Prealbumin
Amyloid Neuropathies, Familial
Amyloidosis, Familial
Online Access:http://www.thieme-connect.de/DOI/DOI?10.1055/s-0044-1793936
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http://www.thieme-connect.de/DOI/DOI?10.1055/s-0044-1793936

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