Cardiac-Specific Gene Editing via an AAV9-Tnnt2-SaCas9-miR122TS Vector

The adeno-associated virus serotype 9 (AAV9)-delivered gene expression driven by the cardiac troponin T (Tnnt2) promoter is broadly considered to be cardiac-specific. However, in cases where low AAV expression is sufficient to trigger a profound biological effect in CRISPR/Cas9 gene editing, the ect...

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Bibliographic Details
Main Authors: Luzi Yang, Congting Guo, Yueshen Sun, Yuxuan Guo
Format: Article
Language:English
Published: Bio-protocol LLC 2025-03-01
Series:Bio-Protocol
Online Access:https://bio-protocol.org/en/bpdetail?id=5235&type=0
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