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"NPC2"
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Endothelial and neuronal engagement by AAV-BR1 gene therapy alleviates neurological symptoms and lipid deposition in a mouse model of Niemann-Pick type C2
by
Charlotte Laurfelt Munch Rasmussen
,
Signe Frost Frederiksen
,
Christian Würtz Heegaard
,
Maj Schneider Thomsen
,
Eva Hede
,
Bartosz Laczek
,
Jakob Körbelin
,
Daniel Wüstner
,
Louiza Bohn Thomsen
,
Markus Schwaninger
,
Ole N. Jensen
,
Torben Moos
,
Annette Burkhart
Published 2025-01-01
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Institution
Kabale University
1 results
1
Format
Article
1 results
1
Author
Annette Burkhart
1 results
1
Bartosz Laczek
1 results
1
Charlotte Laurfelt Munch Rasmussen
1 results
1
Christian Würtz Heegaard
1 results
1
Daniel Wüstner
1 results
1
Eva Hede
1 results
1
Jakob Körbelin
1 results
1
Louiza Bohn Thomsen
1 results
1
Maj Schneider Thomsen
1 results
1
Markus Schwaninger
1 results
1
Ole N. Jensen
1 results
1
Signe Frost Frederiksen
1 results
1
Torben Moos
1 results
1
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Language
English
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1
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