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1
Niemann-pick disease with visceral and pulmonary involvement in a resource limited setting: A rare case report
Published 2025-03-01Subjects: Get full text
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2
Case Report: Two years of compassionate use with Olipudase-alfa in a child with neurovisceral acid sphingomyelinase deficiency
Published 2025-01-01Subjects: “…acid sphingomyelinase deficiency…”
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