Towards a one‐time cure for Fabry disease: Lentivirus‐mediated haematopoietic stem and progenitor cell gene therapy

Towards a one‐time cure for Fabry disease: Lentivirus‐mediated haematopoietic stem and progenitor cell gene therapy

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Bibliographic Details
Main Author:	Rina Kansal
Format:	Article
Language:	English
Published:	Wiley 2025-04-01
Series:	Clinical and Translational Discovery
Subjects:	α‐galactosidase A deficiency disease clinical trial Fabry‒Anderson disease gene therapy genetic disease haematopoietic cells
Online Access:	https://doi.org/10.1002/ctd2.70042
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