Blocking cancer-fibroblast mutualism inhibits proliferation of endocrine therapy resistant breast cancer

Abstract In early-stage estrogen receptor-positive (ER + ) breast cancer, resistance to endocrine therapy (ET) and CDK4/6 inhibitors (CDK4/6i) often involve a shift away from estrogen-driven proliferation. The nature and source of compensatory growth signals driving cancer proliferation remain unkno...

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Main Authors: Jason I Griffiths, Feng Chi, Elena Farmaki, Eric F Medina, Patrick A Cosgrove, Kimya L Karimi, Jinfeng Chen, Vince K Grolmusz, Frederick R Adler, Qamar J Khan, Aritro Nath, Jeffrey T Chang, Andrea H Bild
Format: Article
Language:English
Published: Springer Nature 2025-05-01
Series:Molecular Systems Biology
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Online Access:https://doi.org/10.1038/s44320-025-00104-6
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author Jason I Griffiths
Feng Chi
Elena Farmaki
Eric F Medina
Patrick A Cosgrove
Kimya L Karimi
Jinfeng Chen
Vince K Grolmusz
Frederick R Adler
Qamar J Khan
Aritro Nath
Jeffrey T Chang
Andrea H Bild
author_facet Jason I Griffiths
Feng Chi
Elena Farmaki
Eric F Medina
Patrick A Cosgrove
Kimya L Karimi
Jinfeng Chen
Vince K Grolmusz
Frederick R Adler
Qamar J Khan
Aritro Nath
Jeffrey T Chang
Andrea H Bild
author_sort Jason I Griffiths
collection DOAJ
description Abstract In early-stage estrogen receptor-positive (ER + ) breast cancer, resistance to endocrine therapy (ET) and CDK4/6 inhibitors (CDK4/6i) often involve a shift away from estrogen-driven proliferation. The nature and source of compensatory growth signals driving cancer proliferation remain unknown but represent direct therapeutic targets of resistant cells. By analyzing single-cell RNA-sequencing data from serial biopsies of patient tumors, we elucidated compensatory growth signaling pathways activated in ET + CDK4/6i-resistant cancer cells, along with the intercellular growth signal communications within the tumor microenvironment. In most patient tumors, resistant cancer cells increased ERBB growth pathway activity during treatment, only partially through ERBB receptor upregulation. Concurrently, fibroblasts within the tumor increased ERBB ligand communication with cancer cells, as they differentiated to a proliferative and mesenchymal phenotype in response to TGF $$\beta$$ β signals from cancer cells. In vitro model systems demonstrated molecularly how therapy induces a mutualistic cycle of crosstalk between cancer cells and fibroblasts, fostering a growth factor-rich tumor microenvironment circumventing estrogen reliance. We show that ERBB inhibition can break this cancer-fibroblasts mutualism, targeting an acquired sensitivity of resistant cancer cells.
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spelling doaj-art-e37e7ccbb4cb4c7b99ec431e1fdb44402025-08-20T03:04:21ZengSpringer NatureMolecular Systems Biology1744-42922025-05-0121782585510.1038/s44320-025-00104-6Blocking cancer-fibroblast mutualism inhibits proliferation of endocrine therapy resistant breast cancerJason I Griffiths0Feng Chi1Elena Farmaki2Eric F Medina3Patrick A Cosgrove4Kimya L Karimi5Jinfeng Chen6Vince K Grolmusz7Frederick R Adler8Qamar J Khan9Aritro Nath10Jeffrey T Chang11Andrea H Bild12Department of Medical Oncology & Therapeutics, City of Hope National Medical CenterDepartment of Medical Oncology & Therapeutics, City of Hope National Medical CenterDepartment of Medical Oncology & Therapeutics, City of Hope National Medical CenterDepartment of Medical Oncology & Therapeutics, City of Hope National Medical CenterDepartment of Medical Oncology & Therapeutics, City of Hope National Medical CenterDepartment of Medical Oncology & Therapeutics, City of Hope National Medical CenterDepartment of Medical Oncology & Therapeutics, City of Hope National Medical CenterDepartment of Medical Oncology & Therapeutics, City of Hope National Medical CenterDepartment of Mathematics, University of Utah 155 South 1400 EastDivision of Medical Oncology, Department of Internal Medicine, The University of Kansas Medical CenterDepartment of Medical Oncology & Therapeutics, City of Hope National Medical CenterDepartment of Integrative Biology and Pharmacology, School of Medicine, School of Biomedical Informatics, UT Health Science Center at HoustonDepartment of Medical Oncology & Therapeutics, City of Hope National Medical CenterAbstract In early-stage estrogen receptor-positive (ER + ) breast cancer, resistance to endocrine therapy (ET) and CDK4/6 inhibitors (CDK4/6i) often involve a shift away from estrogen-driven proliferation. The nature and source of compensatory growth signals driving cancer proliferation remain unknown but represent direct therapeutic targets of resistant cells. By analyzing single-cell RNA-sequencing data from serial biopsies of patient tumors, we elucidated compensatory growth signaling pathways activated in ET + CDK4/6i-resistant cancer cells, along with the intercellular growth signal communications within the tumor microenvironment. In most patient tumors, resistant cancer cells increased ERBB growth pathway activity during treatment, only partially through ERBB receptor upregulation. Concurrently, fibroblasts within the tumor increased ERBB ligand communication with cancer cells, as they differentiated to a proliferative and mesenchymal phenotype in response to TGF $$\beta$$ β signals from cancer cells. In vitro model systems demonstrated molecularly how therapy induces a mutualistic cycle of crosstalk between cancer cells and fibroblasts, fostering a growth factor-rich tumor microenvironment circumventing estrogen reliance. We show that ERBB inhibition can break this cancer-fibroblasts mutualism, targeting an acquired sensitivity of resistant cancer cells.https://doi.org/10.1038/s44320-025-00104-6Endocrine ResistanceCancer-fibroblast-mutualismERBB SignalingTME-communication
spellingShingle Jason I Griffiths
Feng Chi
Elena Farmaki
Eric F Medina
Patrick A Cosgrove
Kimya L Karimi
Jinfeng Chen
Vince K Grolmusz
Frederick R Adler
Qamar J Khan
Aritro Nath
Jeffrey T Chang
Andrea H Bild
Blocking cancer-fibroblast mutualism inhibits proliferation of endocrine therapy resistant breast cancer
Molecular Systems Biology
Endocrine Resistance
Cancer-fibroblast-mutualism
ERBB Signaling
TME-communication
title Blocking cancer-fibroblast mutualism inhibits proliferation of endocrine therapy resistant breast cancer
title_full Blocking cancer-fibroblast mutualism inhibits proliferation of endocrine therapy resistant breast cancer
title_fullStr Blocking cancer-fibroblast mutualism inhibits proliferation of endocrine therapy resistant breast cancer
title_full_unstemmed Blocking cancer-fibroblast mutualism inhibits proliferation of endocrine therapy resistant breast cancer
title_short Blocking cancer-fibroblast mutualism inhibits proliferation of endocrine therapy resistant breast cancer
title_sort blocking cancer fibroblast mutualism inhibits proliferation of endocrine therapy resistant breast cancer
topic Endocrine Resistance
Cancer-fibroblast-mutualism
ERBB Signaling
TME-communication
url https://doi.org/10.1038/s44320-025-00104-6
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