Antisense oligonucleotide-mediated exon 27 skipping restores dysferlin function in dysferlinopathy patient-derived muscle cells
Saved in:
| Main Author: | |
|---|---|
| Format: | Article |
| Language: | English |
| Published: |
Elsevier
2025-03-01
|
| Series: | Molecular Therapy: Nucleic Acids |
| Online Access: | http://www.sciencedirect.com/science/article/pii/S2162253125000162 |
| Tags: |
Add Tag
No Tags, Be the first to tag this record!
|
| _version_ | 1832540428103057408 |
|---|---|
| author | Naoki Suzuki |
| author_facet | Naoki Suzuki |
| author_sort | Naoki Suzuki |
| collection | DOAJ |
| format | Article |
| id | doaj-art-e322723452a0400094cb1cc804921d96 |
| institution | Kabale University |
| issn | 2162-2531 |
| language | English |
| publishDate | 2025-03-01 |
| publisher | Elsevier |
| record_format | Article |
| series | Molecular Therapy: Nucleic Acids |
| spelling | doaj-art-e322723452a0400094cb1cc804921d962025-02-05T04:31:45ZengElsevierMolecular Therapy: Nucleic Acids2162-25312025-03-01361102462Antisense oligonucleotide-mediated exon 27 skipping restores dysferlin function in dysferlinopathy patient-derived muscle cellsNaoki Suzuki0Department of Rehabilitation Medicine, Tohoku University Graduate School of Medicine, Sendai, Japan; Department of Rehabilitation, Tohoku Kosai Hospital, Sendai, Japan; Corresponding author: Naoki Suzuki, Department of Rehabilitation Medicine, Tohoku University Graduate School of Medicine, Sendai, Japan.http://www.sciencedirect.com/science/article/pii/S2162253125000162 |
| spellingShingle | Naoki Suzuki Antisense oligonucleotide-mediated exon 27 skipping restores dysferlin function in dysferlinopathy patient-derived muscle cells Molecular Therapy: Nucleic Acids |
| title | Antisense oligonucleotide-mediated exon 27 skipping restores dysferlin function in dysferlinopathy patient-derived muscle cells |
| title_full | Antisense oligonucleotide-mediated exon 27 skipping restores dysferlin function in dysferlinopathy patient-derived muscle cells |
| title_fullStr | Antisense oligonucleotide-mediated exon 27 skipping restores dysferlin function in dysferlinopathy patient-derived muscle cells |
| title_full_unstemmed | Antisense oligonucleotide-mediated exon 27 skipping restores dysferlin function in dysferlinopathy patient-derived muscle cells |
| title_short | Antisense oligonucleotide-mediated exon 27 skipping restores dysferlin function in dysferlinopathy patient-derived muscle cells |
| title_sort | antisense oligonucleotide mediated exon 27 skipping restores dysferlin function in dysferlinopathy patient derived muscle cells |
| url | http://www.sciencedirect.com/science/article/pii/S2162253125000162 |
| work_keys_str_mv | AT naokisuzuki antisenseoligonucleotidemediatedexon27skippingrestoresdysferlinfunctionindysferlinopathypatientderivedmusclecells |