Development of MDM2‐Targeting PROTAC for Advancing Bone Regeneration

Abstract Proteolysis‐targeting chimeras (PROTACs) degrade target proteins through the ubiquitin‐proteasome system. To date, PROTACs are primarily used to treat various diseases; however, they have not been applied in regenerative therapy. Herein, this work introduces MDM2‐targeting PROTACs customize...

Full description

Saved in:
Bibliographic Details
Main Authors: Sol Jeong, Jae‐Kook Cha, Wasim Ahmed, Jaewan Kim, Minsup Kim, Kyung Tae Hong, Wonji Choi, Sunjoo Choi, Tae Hyeon Yoo, Hyun‑Ju An, Seung Chan An, Jaemin Lee, Jimin Choi, Sun‐Young Kim, Jun‐Seok Lee, Soonchul Lee, Junwon Choi, Jin Man Kim
Format: Article
Language:English
Published: Wiley 2025-05-01
Series:Advanced Science
Subjects:
Online Access:https://doi.org/10.1002/advs.202415626
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1850270292784447488
author Sol Jeong
Jae‐Kook Cha
Wasim Ahmed
Jaewan Kim
Minsup Kim
Kyung Tae Hong
Wonji Choi
Sunjoo Choi
Tae Hyeon Yoo
Hyun‑Ju An
Seung Chan An
Jaemin Lee
Jimin Choi
Sun‐Young Kim
Jun‐Seok Lee
Soonchul Lee
Junwon Choi
Jin Man Kim
author_facet Sol Jeong
Jae‐Kook Cha
Wasim Ahmed
Jaewan Kim
Minsup Kim
Kyung Tae Hong
Wonji Choi
Sunjoo Choi
Tae Hyeon Yoo
Hyun‑Ju An
Seung Chan An
Jaemin Lee
Jimin Choi
Sun‐Young Kim
Jun‐Seok Lee
Soonchul Lee
Junwon Choi
Jin Man Kim
author_sort Sol Jeong
collection DOAJ
description Abstract Proteolysis‐targeting chimeras (PROTACs) degrade target proteins through the ubiquitin‐proteasome system. To date, PROTACs are primarily used to treat various diseases; however, they have not been applied in regenerative therapy. Herein, this work introduces MDM2‐targeting PROTACs customized for application in bone regeneration. An MDM2‐PROTAC library is constructed by combining Nutlin‐3 and CRBN ligands with various linker designs. Through a multistep validation process, this work develops MDM2‐PROTACs (CL144 and CL174) that presented potent degradation efficiency and a robust inductive effect on the biomineralization. Next, this work performs whole‐transcriptome analysis to dissect the biological effects of the CL144, and reveals the upregulation of osteogenic marker genes. Furthermore, CL144 effectively induced bone regeneration in bone graft and ovariectomy (OVX) models after local and systemic administration, respectively. In the OVX model, the combination treatment with CL144 and alendronate induced a synergistic effect. Overall, this study demonstrates the promising role of MDM2‐PROTAC in promoting bone regeneration, marking the first step toward expanding the application of the PROTAC technology.
format Article
id doaj-art-db6b5ee5eb3c4c0b8e8cc4f656dd2daa
institution OA Journals
issn 2198-3844
language English
publishDate 2025-05-01
publisher Wiley
record_format Article
series Advanced Science
spelling doaj-art-db6b5ee5eb3c4c0b8e8cc4f656dd2daa2025-08-20T01:52:42ZengWileyAdvanced Science2198-38442025-05-011219n/an/a10.1002/advs.202415626Development of MDM2‐Targeting PROTAC for Advancing Bone RegenerationSol Jeong0Jae‐Kook Cha1Wasim Ahmed2Jaewan Kim3Minsup Kim4Kyung Tae Hong5Wonji Choi6Sunjoo Choi7Tae Hyeon Yoo8Hyun‑Ju An9Seung Chan An10Jaemin Lee11Jimin Choi12Sun‐Young Kim13Jun‐Seok Lee14Soonchul Lee15Junwon Choi16Jin Man Kim17Department of Oral Microbiology and Immunology School of Dentistry and Dental Research Institute Seoul National University Seoul 08826 Republic of KoreaDepartment of Periodontology Research Institute of Periodontal Regeneration College of Dentistry Yonsei University Seoul 03722 Republic of KoreaDepartment of Molecular Science and Technology Ajou University Gyeonggi‐do 16499 Republic of KoreaDepartment of Molecular Science and Technology Ajou University Gyeonggi‐do 16499 Republic of KoreaTARS Scientific Seoul 01717 Republic of KoreaDepartment of Pharmacology Korea University College of Medicine Korea University Seoul 02841 Republic of KoreaDepartment of Molecular Science and Technology Ajou University Gyeonggi‐do 16499 Republic of KoreaDepartment of Molecular Science and Technology Ajou University Gyeonggi‐do 16499 Republic of KoreaDepartment of Molecular Science and Technology Ajou University Gyeonggi‐do 16499 Republic of KoreaDepartment of Orthopaedic Surgery CHA Bundang Medical Center CHA University School of Medicine Gyeonggi‐do 13488 Republic of KoreaDepartment of Orthopaedic Surgery CHA Bundang Medical Center CHA University School of Medicine Gyeonggi‐do 13488 Republic of KoreaDepartment of Orthopaedic Surgery CHA Bundang Medical Center CHA University School of Medicine Gyeonggi‐do 13488 Republic of KoreaDepartment of Periodontology Research Institute of Periodontal Regeneration College of Dentistry Yonsei University Seoul 03722 Republic of KoreaDepartment of Conservative Dentistry and Dental Research Institute School of Dentistry Seoul National University Seoul 08826 Republic of KoreaDepartment of Pharmacology Korea University College of Medicine Korea University Seoul 02841 Republic of KoreaDepartment of Orthopaedic Surgery CHA Bundang Medical Center CHA University School of Medicine Gyeonggi‐do 13488 Republic of KoreaDepartment of Molecular Science and Technology Ajou University Gyeonggi‐do 16499 Republic of KoreaDepartment of Oral Microbiology and Immunology School of Dentistry and Dental Research Institute Seoul National University Seoul 08826 Republic of KoreaAbstract Proteolysis‐targeting chimeras (PROTACs) degrade target proteins through the ubiquitin‐proteasome system. To date, PROTACs are primarily used to treat various diseases; however, they have not been applied in regenerative therapy. Herein, this work introduces MDM2‐targeting PROTACs customized for application in bone regeneration. An MDM2‐PROTAC library is constructed by combining Nutlin‐3 and CRBN ligands with various linker designs. Through a multistep validation process, this work develops MDM2‐PROTACs (CL144 and CL174) that presented potent degradation efficiency and a robust inductive effect on the biomineralization. Next, this work performs whole‐transcriptome analysis to dissect the biological effects of the CL144, and reveals the upregulation of osteogenic marker genes. Furthermore, CL144 effectively induced bone regeneration in bone graft and ovariectomy (OVX) models after local and systemic administration, respectively. In the OVX model, the combination treatment with CL144 and alendronate induced a synergistic effect. Overall, this study demonstrates the promising role of MDM2‐PROTAC in promoting bone regeneration, marking the first step toward expanding the application of the PROTAC technology.https://doi.org/10.1002/advs.202415626boneMDM2osteoporosisPROTACregenerative medicine
spellingShingle Sol Jeong
Jae‐Kook Cha
Wasim Ahmed
Jaewan Kim
Minsup Kim
Kyung Tae Hong
Wonji Choi
Sunjoo Choi
Tae Hyeon Yoo
Hyun‑Ju An
Seung Chan An
Jaemin Lee
Jimin Choi
Sun‐Young Kim
Jun‐Seok Lee
Soonchul Lee
Junwon Choi
Jin Man Kim
Development of MDM2‐Targeting PROTAC for Advancing Bone Regeneration
Advanced Science
bone
MDM2
osteoporosis
PROTAC
regenerative medicine
title Development of MDM2‐Targeting PROTAC for Advancing Bone Regeneration
title_full Development of MDM2‐Targeting PROTAC for Advancing Bone Regeneration
title_fullStr Development of MDM2‐Targeting PROTAC for Advancing Bone Regeneration
title_full_unstemmed Development of MDM2‐Targeting PROTAC for Advancing Bone Regeneration
title_short Development of MDM2‐Targeting PROTAC for Advancing Bone Regeneration
title_sort development of mdm2 targeting protac for advancing bone regeneration
topic bone
MDM2
osteoporosis
PROTAC
regenerative medicine
url https://doi.org/10.1002/advs.202415626
work_keys_str_mv AT soljeong developmentofmdm2targetingprotacforadvancingboneregeneration
AT jaekookcha developmentofmdm2targetingprotacforadvancingboneregeneration
AT wasimahmed developmentofmdm2targetingprotacforadvancingboneregeneration
AT jaewankim developmentofmdm2targetingprotacforadvancingboneregeneration
AT minsupkim developmentofmdm2targetingprotacforadvancingboneregeneration
AT kyungtaehong developmentofmdm2targetingprotacforadvancingboneregeneration
AT wonjichoi developmentofmdm2targetingprotacforadvancingboneregeneration
AT sunjoochoi developmentofmdm2targetingprotacforadvancingboneregeneration
AT taehyeonyoo developmentofmdm2targetingprotacforadvancingboneregeneration
AT hyunjuan developmentofmdm2targetingprotacforadvancingboneregeneration
AT seungchanan developmentofmdm2targetingprotacforadvancingboneregeneration
AT jaeminlee developmentofmdm2targetingprotacforadvancingboneregeneration
AT jiminchoi developmentofmdm2targetingprotacforadvancingboneregeneration
AT sunyoungkim developmentofmdm2targetingprotacforadvancingboneregeneration
AT junseoklee developmentofmdm2targetingprotacforadvancingboneregeneration
AT soonchullee developmentofmdm2targetingprotacforadvancingboneregeneration
AT junwonchoi developmentofmdm2targetingprotacforadvancingboneregeneration
AT jinmankim developmentofmdm2targetingprotacforadvancingboneregeneration