Population pharmacokinetics of high-dose methotrexate in patients with primary central nervous system lymphoma

ObjectiveMethotrexate (MTX) serves as a cornerstone therapy for primary central nervous system lymphoma (PCNSL). However, the considerable intra- and inter-individual variability in its pharmacokinetic and therapeutic efficacy poses significant challenges to clinical application. This study aims to...

Full description

Saved in:
Bibliographic Details
Main Authors: Shifeng Wei, Sitian Zhang, Dan Wang, Dongjie Zhang, Qian Lu, Jiayi Mo, Zhilin Yang, Leyi Guan, Yingjun He, Zhigang Zhao, Shenghui Mei
Format: Article
Language:English
Published: Frontiers Media S.A. 2025-05-01
Series:Frontiers in Pharmacology
Subjects:
Online Access:https://www.frontiersin.org/articles/10.3389/fphar.2025.1578033/full
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1850132525459963904
author Shifeng Wei
Shifeng Wei
Sitian Zhang
Dan Wang
Dan Wang
Dongjie Zhang
Qian Lu
Jiayi Mo
Jiayi Mo
Zhilin Yang
Zhilin Yang
Leyi Guan
Yingjun He
Zhigang Zhao
Zhigang Zhao
Shenghui Mei
Shenghui Mei
author_facet Shifeng Wei
Shifeng Wei
Sitian Zhang
Dan Wang
Dan Wang
Dongjie Zhang
Qian Lu
Jiayi Mo
Jiayi Mo
Zhilin Yang
Zhilin Yang
Leyi Guan
Yingjun He
Zhigang Zhao
Zhigang Zhao
Shenghui Mei
Shenghui Mei
author_sort Shifeng Wei
collection DOAJ
description ObjectiveMethotrexate (MTX) serves as a cornerstone therapy for primary central nervous system lymphoma (PCNSL). However, the considerable intra- and inter-individual variability in its pharmacokinetic and therapeutic efficacy poses significant challenges to clinical application. This study aims to employ population pharmacokinetic (PPK) models to investigate the pharmacokinetics of MTX in Chinese patients with PCNSL, thereby facilitating personalized therapeutic strategies for these patients.MethodA retrospective dataset comprising 6074 MTX plasma concentrations from 752 adult patients with PCNSL receiving high-dose methotrexate (HD-MTX) therapy was employed to construct the PPK model, utilizing the nonlinear mixed-effects modeling approach. The pharmacokinetics of MTX were characterized using a three-compartment model in conjunction with a proportional residual model. Covariate effects on model parameters were evaluated using forward addition and backward elimination approaches. Model performance was assessed through goodness-of-fit, bootstrap analysis, and visual predictive checks.ResultIn the final PPK models, the estimated glomerular filtration rate (eGFR), blood urea nitrogen (BUN), alanine aminotransferase (ALT), and a combined genotype of ABCC-ABCG-ADORA2A were identified as significant covariates impacting the clearance (CL) of MTX. Additionally, total protein (TP) was found to be a significant covariate influencing inter-compartmental clearance (Q). The relationship between pharmacokinetic parameters and covariates was quantified as follows: CL (L/h) = 8.45×(eGFR⁄101.8)0.67×(BUN⁄4.6)−0.08×(ALT⁄25)0.03×a (a = 0.91 for gene-model if ABCC-ABCG-ADORA2A mutation, otherwise a = 1); Q1 (L/h) = 0.04×(TP⁄58)b (b = −1.68 for nongene-model and b = −1.72 for gene-model). Bootstrap analysis and visual predictive checks demonstrated the stability and adequate predictive capacity of the final PPK models.ConclusionIn managing HD-MTX therapy for PCNSL patients, it is essential to consider pharmacokinetic factors such as eGFR, BUN, ALT, TP, and genetic polymorphisms. The PPK models developed will aid in optimizing and personalizing HD-MTX treatment for PCNSL patients.
format Article
id doaj-art-c6545ae8d7de429c8e481df4561d95f9
institution OA Journals
issn 1663-9812
language English
publishDate 2025-05-01
publisher Frontiers Media S.A.
record_format Article
series Frontiers in Pharmacology
spelling doaj-art-c6545ae8d7de429c8e481df4561d95f92025-08-20T02:32:11ZengFrontiers Media S.A.Frontiers in Pharmacology1663-98122025-05-011610.3389/fphar.2025.15780331578033Population pharmacokinetics of high-dose methotrexate in patients with primary central nervous system lymphomaShifeng Wei0Shifeng Wei1Sitian Zhang2Dan Wang3Dan Wang4Dongjie Zhang5Qian Lu6Jiayi Mo7Jiayi Mo8Zhilin Yang9Zhilin Yang10Leyi Guan11Yingjun He12Zhigang Zhao13Zhigang Zhao14Shenghui Mei15Shenghui Mei16Department of Pharmacy, Beijing Tiantan Hospital, Capital Medical University, Beijing, ChinaDepartment of Clinical Pharmacology, College of Pharmaceutical Sciences, Capital Medical University, Beijing, ChinaSchool of Basic Medical Sciences, Capital Medical University, Beijing, ChinaDepartment of Pharmacy, Beijing Tiantan Hospital, Capital Medical University, Beijing, ChinaDepartment of Clinical Pharmacology, College of Pharmaceutical Sciences, Capital Medical University, Beijing, ChinaDepartment of Pharmacy, Beijing Tiantan Hospital, Capital Medical University, Beijing, ChinaDepartment of Pharmacy, Bijie Maternal and Child Health Hospital, Bijie, Guizhou, ChinaDepartment of Pharmacy, Beijing Tiantan Hospital, Capital Medical University, Beijing, ChinaDepartment of Clinical Pharmacology, College of Pharmaceutical Sciences, Capital Medical University, Beijing, ChinaDepartment of Pharmacy, Beijing Tiantan Hospital, Capital Medical University, Beijing, ChinaDepartment of Clinical Pharmacology, College of Pharmaceutical Sciences, Capital Medical University, Beijing, ChinaDepartment of Clinical Pharmacology, College of Pharmaceutical Sciences, Capital Medical University, Beijing, ChinaDepartment of Pharmacy, Bijie Maternal and Child Health Hospital, Bijie, Guizhou, ChinaDepartment of Pharmacy, Beijing Tiantan Hospital, Capital Medical University, Beijing, ChinaDepartment of Clinical Pharmacology, College of Pharmaceutical Sciences, Capital Medical University, Beijing, ChinaDepartment of Pharmacy, Beijing Tiantan Hospital, Capital Medical University, Beijing, ChinaDepartment of Clinical Pharmacology, College of Pharmaceutical Sciences, Capital Medical University, Beijing, ChinaObjectiveMethotrexate (MTX) serves as a cornerstone therapy for primary central nervous system lymphoma (PCNSL). However, the considerable intra- and inter-individual variability in its pharmacokinetic and therapeutic efficacy poses significant challenges to clinical application. This study aims to employ population pharmacokinetic (PPK) models to investigate the pharmacokinetics of MTX in Chinese patients with PCNSL, thereby facilitating personalized therapeutic strategies for these patients.MethodA retrospective dataset comprising 6074 MTX plasma concentrations from 752 adult patients with PCNSL receiving high-dose methotrexate (HD-MTX) therapy was employed to construct the PPK model, utilizing the nonlinear mixed-effects modeling approach. The pharmacokinetics of MTX were characterized using a three-compartment model in conjunction with a proportional residual model. Covariate effects on model parameters were evaluated using forward addition and backward elimination approaches. Model performance was assessed through goodness-of-fit, bootstrap analysis, and visual predictive checks.ResultIn the final PPK models, the estimated glomerular filtration rate (eGFR), blood urea nitrogen (BUN), alanine aminotransferase (ALT), and a combined genotype of ABCC-ABCG-ADORA2A were identified as significant covariates impacting the clearance (CL) of MTX. Additionally, total protein (TP) was found to be a significant covariate influencing inter-compartmental clearance (Q). The relationship between pharmacokinetic parameters and covariates was quantified as follows: CL (L/h) = 8.45×(eGFR⁄101.8)0.67×(BUN⁄4.6)−0.08×(ALT⁄25)0.03×a (a = 0.91 for gene-model if ABCC-ABCG-ADORA2A mutation, otherwise a = 1); Q1 (L/h) = 0.04×(TP⁄58)b (b = −1.68 for nongene-model and b = −1.72 for gene-model). Bootstrap analysis and visual predictive checks demonstrated the stability and adequate predictive capacity of the final PPK models.ConclusionIn managing HD-MTX therapy for PCNSL patients, it is essential to consider pharmacokinetic factors such as eGFR, BUN, ALT, TP, and genetic polymorphisms. The PPK models developed will aid in optimizing and personalizing HD-MTX treatment for PCNSL patients.https://www.frontiersin.org/articles/10.3389/fphar.2025.1578033/fullmethotrexateprimary central nervous system lymphomapopulation pharmacokinetic modelnonlinear mixed-effects modelingestimated glomerular filtration rateblood urea nitrogen
spellingShingle Shifeng Wei
Shifeng Wei
Sitian Zhang
Dan Wang
Dan Wang
Dongjie Zhang
Qian Lu
Jiayi Mo
Jiayi Mo
Zhilin Yang
Zhilin Yang
Leyi Guan
Yingjun He
Zhigang Zhao
Zhigang Zhao
Shenghui Mei
Shenghui Mei
Population pharmacokinetics of high-dose methotrexate in patients with primary central nervous system lymphoma
Frontiers in Pharmacology
methotrexate
primary central nervous system lymphoma
population pharmacokinetic model
nonlinear mixed-effects modeling
estimated glomerular filtration rate
blood urea nitrogen
title Population pharmacokinetics of high-dose methotrexate in patients with primary central nervous system lymphoma
title_full Population pharmacokinetics of high-dose methotrexate in patients with primary central nervous system lymphoma
title_fullStr Population pharmacokinetics of high-dose methotrexate in patients with primary central nervous system lymphoma
title_full_unstemmed Population pharmacokinetics of high-dose methotrexate in patients with primary central nervous system lymphoma
title_short Population pharmacokinetics of high-dose methotrexate in patients with primary central nervous system lymphoma
title_sort population pharmacokinetics of high dose methotrexate in patients with primary central nervous system lymphoma
topic methotrexate
primary central nervous system lymphoma
population pharmacokinetic model
nonlinear mixed-effects modeling
estimated glomerular filtration rate
blood urea nitrogen
url https://www.frontiersin.org/articles/10.3389/fphar.2025.1578033/full
work_keys_str_mv AT shifengwei populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT shifengwei populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT sitianzhang populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT danwang populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT danwang populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT dongjiezhang populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT qianlu populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT jiayimo populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT jiayimo populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT zhilinyang populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT zhilinyang populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT leyiguan populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT yingjunhe populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT zhigangzhao populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT zhigangzhao populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT shenghuimei populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma
AT shenghuimei populationpharmacokineticsofhighdosemethotrexateinpatientswithprimarycentralnervoussystemlymphoma