Evaluation of Organoid‐Derived Exosomal microRNA as Liquid Biopsy for Colorectal Cancer: A Multicenter Cross‐Sectional Study

ABSTRACT Exosomal microRNAs (miRNAs) are candidates for liquid biopsies. Organoid culture systems enable long‐term expansion of the colon epithelium. This study evaluated exosomal miRNAs from colorectal cancer organoids for liquid biopsy. Organoids were established from normal colon and colorectal c...

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Main Authors: Atsuhiro Sasaki, Masatake Kuroha, Masaki Tosa, Seiichi Takahashi, Shinya Oomori, Eiki Nomura, Tatsuya Kikuchi, Motoyuki Onodera, Yuichiro Sato, Teruko Miyazawa, Hirofumi Chiba, Naonobu Yokoyama, Jun Kusaka, Daisuke Okamoto, Tomoyuki Handa, Mikako Sugimura, Masahiro Iwabuchi, Keiichiro Hiramoto, Hidekazu Shirota, Hideya Iwaki, Hiroshi Nagai, Yusuke Shimoyama, Takeo Naito, Rintaro Moroi, Hisashi Shiga, Yoichi Kakuta, Yoshitaka Kinouchi, Atsushi Masamune
Format: Article
Language:English
Published: Wiley 2025-06-01
Series:Clinical and Translational Science
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Online Access:https://doi.org/10.1111/cts.70270
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author Atsuhiro Sasaki
Masatake Kuroha
Masaki Tosa
Seiichi Takahashi
Shinya Oomori
Eiki Nomura
Tatsuya Kikuchi
Motoyuki Onodera
Yuichiro Sato
Teruko Miyazawa
Hirofumi Chiba
Naonobu Yokoyama
Jun Kusaka
Daisuke Okamoto
Tomoyuki Handa
Mikako Sugimura
Masahiro Iwabuchi
Keiichiro Hiramoto
Hidekazu Shirota
Hideya Iwaki
Hiroshi Nagai
Yusuke Shimoyama
Takeo Naito
Rintaro Moroi
Hisashi Shiga
Yoichi Kakuta
Yoshitaka Kinouchi
Atsushi Masamune
author_facet Atsuhiro Sasaki
Masatake Kuroha
Masaki Tosa
Seiichi Takahashi
Shinya Oomori
Eiki Nomura
Tatsuya Kikuchi
Motoyuki Onodera
Yuichiro Sato
Teruko Miyazawa
Hirofumi Chiba
Naonobu Yokoyama
Jun Kusaka
Daisuke Okamoto
Tomoyuki Handa
Mikako Sugimura
Masahiro Iwabuchi
Keiichiro Hiramoto
Hidekazu Shirota
Hideya Iwaki
Hiroshi Nagai
Yusuke Shimoyama
Takeo Naito
Rintaro Moroi
Hisashi Shiga
Yoichi Kakuta
Yoshitaka Kinouchi
Atsushi Masamune
author_sort Atsuhiro Sasaki
collection DOAJ
description ABSTRACT Exosomal microRNAs (miRNAs) are candidates for liquid biopsies. Organoid culture systems enable long‐term expansion of the colon epithelium. This study evaluated exosomal miRNAs from colorectal cancer organoids for liquid biopsy. Organoids were established from normal colon and colorectal cancer tissues. Exosomes were isolated from conditioned media. miRNAs were extracted from exosomes and compared using microarray analysis. Exosomal miRNAs expression levels in the sera of healthy patients and patients with colorectal cancer were compared at a single institution. The multicenter study was validated using miRNAs upregulated in the serum of colorectal cancer patients, along with exosomal miRNAs reported to be upregulated in colorectal adenoma organoids and sera. A total of 44 exosomal miRNAs were commonly expressed in both normal colorectal epithelial cells and colorectal cancer organoids, whereas 59 were exclusively expressed in colorectal cancer organoids. In a single‐center cohort study, two exosomal miRNAs (miR‐4284 and miR‐5100) were upregulated in the serum of colorectal cancer patients. In a multicenter study, four exosomal miRNAs (miR‐4284, miR‐5100, miR‐1246, and miR‐1290) were upregulated in the serum of patients with colorectal cancer. The combination of these four exosomal miRNAs had comparable diagnostic performance to carcinoembryonic antigen, with an area under the curve of 0.75 (95% confidence interval: 0.65–0.83) versus 0.79 (95% confidence interval: 0.70–0.87). Combining the four miRNAs with carcinoembryonic antigen improved diagnostic accuracy, with an area under the curve of 0.82 (95% confidence interval: 0.74–0.89). Exosomal miRNAs derived from colorectal cancer organoids can serve as diagnostic biomarkers for colorectal cancer.
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spelling doaj-art-b99b9b1ca8c94daa86e194bf2ac157722025-08-20T03:28:00ZengWileyClinical and Translational Science1752-80541752-80622025-06-01186n/an/a10.1111/cts.70270Evaluation of Organoid‐Derived Exosomal microRNA as Liquid Biopsy for Colorectal Cancer: A Multicenter Cross‐Sectional StudyAtsuhiro Sasaki0Masatake Kuroha1Masaki Tosa2Seiichi Takahashi3Shinya Oomori4Eiki Nomura5Tatsuya Kikuchi6Motoyuki Onodera7Yuichiro Sato8Teruko Miyazawa9Hirofumi Chiba10Naonobu Yokoyama11Jun Kusaka12Daisuke Okamoto13Tomoyuki Handa14Mikako Sugimura15Masahiro Iwabuchi16Keiichiro Hiramoto17Hidekazu Shirota18Hideya Iwaki19Hiroshi Nagai20Yusuke Shimoyama21Takeo Naito22Rintaro Moroi23Hisashi Shiga24Yoichi Kakuta25Yoshitaka Kinouchi26Atsushi Masamune27Division of Gastroenterology Tohoku University Graduate School of Medicine Sendai JapanDivision of Gastroenterology Tohoku University Graduate School of Medicine Sendai JapanDepartment of Gastroenterology Iwaki City Medical Center Iwaki JapanDepartment of Gastroenterology Iwaki City Medical Center Iwaki JapanDepartment of Gastroenterology Japanese Red Cross Sendai Hospital Sendai JapanDepartment of Gastroenterology Sendai City Hospital Sendai JapanDepartment of Gastroenterology Sendai City Hospital Sendai JapanDepartment of Gastroenterology Osaki Citizen Hospital Osaki JapanDepartment of Gastroenterology Osaki Citizen Hospital Osaki JapanDepartment of Gastroenterology Japan Community Healthcare Organization, Sendai South Hospital Sendai JapanDepartment of Gastroenterology Iwate Prefectural Isawa Hospital Oshu JapanDepartment of Gastroenterology Iwate Prefectural Iwai Hospital Ichinoseki JapanDepartment of Gastroenterology Miyagi Cancer Center Natori JapanDepartment of Gastroenterology Shirakawa Kosei General Hospital Shirakawa JapanDepartment of Internal Medicine Kurihara Central Hospital Kurihara JapanDepartment of Gastroenterology NHO Sendai Medical Center Sendai JapanDepartment of Gastroenterology NHO Sendai Medical Center Sendai JapanDepartment of Gastroenterology South Miyagi Medical Center Ohgawara JapanDepartment of Medical Oncology Tohoku University Hospital Sendai JapanDivision of Gastroenterology Tohoku University Graduate School of Medicine Sendai JapanDivision of Gastroenterology Tohoku University Graduate School of Medicine Sendai JapanDivision of Gastroenterology Tohoku University Graduate School of Medicine Sendai JapanDivision of Gastroenterology Tohoku University Graduate School of Medicine Sendai JapanDivision of Gastroenterology Tohoku University Graduate School of Medicine Sendai JapanDivision of Gastroenterology Tohoku University Graduate School of Medicine Sendai JapanDivision of Gastroenterology Tohoku University Graduate School of Medicine Sendai JapanStudent Healthcare Center, Institute for Excellence in Higher Education Tohoku University Sendai JapanDivision of Gastroenterology Tohoku University Graduate School of Medicine Sendai JapanABSTRACT Exosomal microRNAs (miRNAs) are candidates for liquid biopsies. Organoid culture systems enable long‐term expansion of the colon epithelium. This study evaluated exosomal miRNAs from colorectal cancer organoids for liquid biopsy. Organoids were established from normal colon and colorectal cancer tissues. Exosomes were isolated from conditioned media. miRNAs were extracted from exosomes and compared using microarray analysis. Exosomal miRNAs expression levels in the sera of healthy patients and patients with colorectal cancer were compared at a single institution. The multicenter study was validated using miRNAs upregulated in the serum of colorectal cancer patients, along with exosomal miRNAs reported to be upregulated in colorectal adenoma organoids and sera. A total of 44 exosomal miRNAs were commonly expressed in both normal colorectal epithelial cells and colorectal cancer organoids, whereas 59 were exclusively expressed in colorectal cancer organoids. In a single‐center cohort study, two exosomal miRNAs (miR‐4284 and miR‐5100) were upregulated in the serum of colorectal cancer patients. In a multicenter study, four exosomal miRNAs (miR‐4284, miR‐5100, miR‐1246, and miR‐1290) were upregulated in the serum of patients with colorectal cancer. The combination of these four exosomal miRNAs had comparable diagnostic performance to carcinoembryonic antigen, with an area under the curve of 0.75 (95% confidence interval: 0.65–0.83) versus 0.79 (95% confidence interval: 0.70–0.87). Combining the four miRNAs with carcinoembryonic antigen improved diagnostic accuracy, with an area under the curve of 0.82 (95% confidence interval: 0.74–0.89). Exosomal miRNAs derived from colorectal cancer organoids can serve as diagnostic biomarkers for colorectal cancer.https://doi.org/10.1111/cts.70270carcinoembryonic antigenmiR‐1246miR‐1290miR‐4284miR‐5100
spellingShingle Atsuhiro Sasaki
Masatake Kuroha
Masaki Tosa
Seiichi Takahashi
Shinya Oomori
Eiki Nomura
Tatsuya Kikuchi
Motoyuki Onodera
Yuichiro Sato
Teruko Miyazawa
Hirofumi Chiba
Naonobu Yokoyama
Jun Kusaka
Daisuke Okamoto
Tomoyuki Handa
Mikako Sugimura
Masahiro Iwabuchi
Keiichiro Hiramoto
Hidekazu Shirota
Hideya Iwaki
Hiroshi Nagai
Yusuke Shimoyama
Takeo Naito
Rintaro Moroi
Hisashi Shiga
Yoichi Kakuta
Yoshitaka Kinouchi
Atsushi Masamune
Evaluation of Organoid‐Derived Exosomal microRNA as Liquid Biopsy for Colorectal Cancer: A Multicenter Cross‐Sectional Study
Clinical and Translational Science
carcinoembryonic antigen
miR‐1246
miR‐1290
miR‐4284
miR‐5100
title Evaluation of Organoid‐Derived Exosomal microRNA as Liquid Biopsy for Colorectal Cancer: A Multicenter Cross‐Sectional Study
title_full Evaluation of Organoid‐Derived Exosomal microRNA as Liquid Biopsy for Colorectal Cancer: A Multicenter Cross‐Sectional Study
title_fullStr Evaluation of Organoid‐Derived Exosomal microRNA as Liquid Biopsy for Colorectal Cancer: A Multicenter Cross‐Sectional Study
title_full_unstemmed Evaluation of Organoid‐Derived Exosomal microRNA as Liquid Biopsy for Colorectal Cancer: A Multicenter Cross‐Sectional Study
title_short Evaluation of Organoid‐Derived Exosomal microRNA as Liquid Biopsy for Colorectal Cancer: A Multicenter Cross‐Sectional Study
title_sort evaluation of organoid derived exosomal microrna as liquid biopsy for colorectal cancer a multicenter cross sectional study
topic carcinoembryonic antigen
miR‐1246
miR‐1290
miR‐4284
miR‐5100
url https://doi.org/10.1111/cts.70270
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