P048: Three year safety experience in children treated with govorestat for classic galactosemia

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Main Authors: Evan Bailey, Riccardo Perfetti, Shoshana Shendelman
Format: Article
Language:English
Published: Elsevier 2025-01-01
Series:Genetics in Medicine Open
Online Access:http://www.sciencedirect.com/science/article/pii/S2949774425009318
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author Evan Bailey
Riccardo Perfetti
Shoshana Shendelman
author_facet Evan Bailey
Riccardo Perfetti
Shoshana Shendelman
author_sort Evan Bailey
collection DOAJ
format Article
id doaj-art-a767ab6e9e3a4d83b1b7bcd3a2756e47
institution DOAJ
issn 2949-7744
language English
publishDate 2025-01-01
publisher Elsevier
record_format Article
series Genetics in Medicine Open
spelling doaj-art-a767ab6e9e3a4d83b1b7bcd3a2756e472025-08-20T03:14:32ZengElsevierGenetics in Medicine Open2949-77442025-01-01310289210.1016/j.gimo.2025.102892P048: Three year safety experience in children treated with govorestat for classic galactosemiaEvan Bailey0Riccardo Perfetti1Shoshana Shendelman2Applied Therapeutics, IncApplied Therapeutics, IncApplied Therapeutics, Inchttp://www.sciencedirect.com/science/article/pii/S2949774425009318
spellingShingle Evan Bailey
Riccardo Perfetti
Shoshana Shendelman
P048: Three year safety experience in children treated with govorestat for classic galactosemia
Genetics in Medicine Open
title P048: Three year safety experience in children treated with govorestat for classic galactosemia
title_full P048: Three year safety experience in children treated with govorestat for classic galactosemia
title_fullStr P048: Three year safety experience in children treated with govorestat for classic galactosemia
title_full_unstemmed P048: Three year safety experience in children treated with govorestat for classic galactosemia
title_short P048: Three year safety experience in children treated with govorestat for classic galactosemia
title_sort p048 three year safety experience in children treated with govorestat for classic galactosemia
url http://www.sciencedirect.com/science/article/pii/S2949774425009318
work_keys_str_mv AT evanbailey p048threeyearsafetyexperienceinchildrentreatedwithgovorestatforclassicgalactosemia
AT riccardoperfetti p048threeyearsafetyexperienceinchildrentreatedwithgovorestatforclassicgalactosemia
AT shoshanashendelman p048threeyearsafetyexperienceinchildrentreatedwithgovorestatforclassicgalactosemia