The burden of Alagille syndrome: uncovering the potential of emerging therapeutics – a comprehensive systematic literature review

The burden of Alagille syndrome: uncovering the potential of emerging therapeutics – a comprehensive systematic literature review

Aim: Alagille syndrome (ALGS) is a rare, cholestatic multiorgan disease associated with bile duct paucity, leading to cholestasis. Clinical symptoms of cholestasis include debilitating pruritus, xanthomas, fatsoluble vitamin deficiencies, growth failure, renal disease and impaired health-related q...

Full description

Saved in:
Bibliographic Details
Main Authors: Philip Bufler, Robin Howard, Lucia Quadrado, Guy Lacey, Jolan Terner-Rosenthal, Andrea Goldstein, Pamela Vig, Deirdre Kelly
Format: Article
Language:English
Published: Becaris Publishing Limited 2025-01-01
Series:Journal of Comparative Effectiveness Research
Subjects:
alagille syndrome
algs
cholestasis
health-related quality of life
pruritus
Tags: Add Tag
No Tags, Be the first to tag this record!

Similar Items

Similar Items