Application of antisense oligonucleotide drugs in amyotrophic lateral sclerosis and Huntington’s disease

Abstract Amyotrophic lateral sclerosis (ALS) and Huntington’s disease (HD) are diverse in clinical presentation and are caused by complex and multiple factors, including genetic mutations and environmental factors. Numerous therapeutic approaches have been developed based on the genetic causes and p...

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Bibliographic Details
Main Authors: Kaili Ou, Qingqing Jia, Dandan Li, Shihua Li, Xiao-Jiang Li, Peng Yin
Format: Article
Language:English
Published: BMC 2025-01-01
Series:Translational Neurodegeneration
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Online Access:https://doi.org/10.1186/s40035-025-00466-9
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