From mechanisms to future therapy: a synopsis of isolated REM sleep behavior disorder as early synuclein-related disease

Abstract Parkinson disease (PD), dementia with Lewy bodies (DLB) and multiple system atrophy are synucleinopathies, characterized by neuronal loss, gliosis and the abnormal deposition of α-synuclein in vulnerable areas of the nervous system. Neurodegeneration begins however several years before clin...

Full description

Saved in:
Bibliographic Details
Main Authors: Ambra Stefani, Elena Antelmi, Dario Arnaldi, Isabelle Arnulf, Emmanuel During, Birgit Högl, Michele M. T. Hu, Alex Iranzo, Russell Luke, John Peever, Ronald B. Postuma, Aleksandar Videnovic, Ziv Gan-Or
Format: Article
Language:English
Published: BMC 2025-02-01
Series:Molecular Neurodegeneration
Online Access:https://doi.org/10.1186/s13024-025-00809-0
Tags: Add Tag
No Tags, Be the first to tag this record!
_version_ 1850024785597169664
author Ambra Stefani
Elena Antelmi
Dario Arnaldi
Isabelle Arnulf
Emmanuel During
Birgit Högl
Michele M. T. Hu
Alex Iranzo
Russell Luke
John Peever
Ronald B. Postuma
Aleksandar Videnovic
Ziv Gan-Or
author_facet Ambra Stefani
Elena Antelmi
Dario Arnaldi
Isabelle Arnulf
Emmanuel During
Birgit Högl
Michele M. T. Hu
Alex Iranzo
Russell Luke
John Peever
Ronald B. Postuma
Aleksandar Videnovic
Ziv Gan-Or
author_sort Ambra Stefani
collection DOAJ
description Abstract Parkinson disease (PD), dementia with Lewy bodies (DLB) and multiple system atrophy are synucleinopathies, characterized by neuronal loss, gliosis and the abnormal deposition of α-synuclein in vulnerable areas of the nervous system. Neurodegeneration begins however several years before clinical onset of motor, cognitive or autonomic symptoms. The isolated form of REM sleep behavior disorder (RBD), a parasomnia with dream enactment behaviors and excessive muscle activity during REM sleep, is an early stage synucleinopathy. The neurophysiological hallmark of RBD is REM sleep without atonia (RWSA), i.e. the loss of physiological muscle atonia during REM sleep. RBD pathophysiology is not fully clarified yet, but clinical and basic science suggest that ɑ-syn pathology begins in the lower brainstem where REM atonia circuits are located, including the sublaterodorsal tegmental/subcoeruleus nucleus and the ventral medulla, then propagates rostrally to brain regions such as the substantia nigra, limbic system, cortex. Genetically, there is only a partial overlap between RBD, PD and DLB, and individuals with iRBD may represent a specific subpopulation. A genome-wide association study identified five loci, which all seem to revolve around the GBA1 pathway. iRBD patients often show subtle motor, cognitive, autonomic and/or sensory signs, neuroimaging alterations as well as biofluid and tissue markers of neurodegeneration (in particular pathologic α-synuclein aggregates), which can be useful for risk stratification. Patients with iRBD represent thus the ideal population for neuroprotective/neuromodulating trials. This review provides insights into these aspects, highlighting and substantiating the central role of iRBD in treatment development strategies for synucleinopathies.
format Article
id doaj-art-6e8fda5c13944f35b1e0dedb7c20c5e3
institution DOAJ
issn 1750-1326
language English
publishDate 2025-02-01
publisher BMC
record_format Article
series Molecular Neurodegeneration
spelling doaj-art-6e8fda5c13944f35b1e0dedb7c20c5e32025-08-20T03:01:00ZengBMCMolecular Neurodegeneration1750-13262025-02-0120111710.1186/s13024-025-00809-0From mechanisms to future therapy: a synopsis of isolated REM sleep behavior disorder as early synuclein-related diseaseAmbra Stefani0Elena Antelmi1Dario Arnaldi2Isabelle Arnulf3Emmanuel During4Birgit Högl5Michele M. T. Hu6Alex Iranzo7Russell Luke8John Peever9Ronald B. Postuma10Aleksandar Videnovic11Ziv Gan-Or12Medical University InnsbruckDIMI Department of Engineering and Medicine of Innovation, University of VeronaClinical Neurophysiology, IRCCS Ospedale Policlinico San MartinoSleep Clinic, Pitié-Salpêtrière Hospital, APHP - Sorbonne UniversityDepartment of Neurology, Icahn School of Medicine at Mount SinaiMedical University InnsbruckDivision of Neurology, Nuffield Department of Clinical Neurosciences, Oxford UniversitySleep Unit, Neurology Service, Hospital Clínic de Barcelona, IDIBAPS, CIBERNED: CB06/05/0018-ISCIII, Universitat de Barcelona,Department of Cell and System Biology, University of TorontoDepartment of Cell and System Biology, University of TorontoDepartment of Neurology and Neurosurgery, McGill UniversityDepartment of Neurology, Massachusetts General Hospital, Harvard Medical SchoolDepartment of Neurology and Neurosurgery, McGill UniversityAbstract Parkinson disease (PD), dementia with Lewy bodies (DLB) and multiple system atrophy are synucleinopathies, characterized by neuronal loss, gliosis and the abnormal deposition of α-synuclein in vulnerable areas of the nervous system. Neurodegeneration begins however several years before clinical onset of motor, cognitive or autonomic symptoms. The isolated form of REM sleep behavior disorder (RBD), a parasomnia with dream enactment behaviors and excessive muscle activity during REM sleep, is an early stage synucleinopathy. The neurophysiological hallmark of RBD is REM sleep without atonia (RWSA), i.e. the loss of physiological muscle atonia during REM sleep. RBD pathophysiology is not fully clarified yet, but clinical and basic science suggest that ɑ-syn pathology begins in the lower brainstem where REM atonia circuits are located, including the sublaterodorsal tegmental/subcoeruleus nucleus and the ventral medulla, then propagates rostrally to brain regions such as the substantia nigra, limbic system, cortex. Genetically, there is only a partial overlap between RBD, PD and DLB, and individuals with iRBD may represent a specific subpopulation. A genome-wide association study identified five loci, which all seem to revolve around the GBA1 pathway. iRBD patients often show subtle motor, cognitive, autonomic and/or sensory signs, neuroimaging alterations as well as biofluid and tissue markers of neurodegeneration (in particular pathologic α-synuclein aggregates), which can be useful for risk stratification. Patients with iRBD represent thus the ideal population for neuroprotective/neuromodulating trials. This review provides insights into these aspects, highlighting and substantiating the central role of iRBD in treatment development strategies for synucleinopathies.https://doi.org/10.1186/s13024-025-00809-0
spellingShingle Ambra Stefani
Elena Antelmi
Dario Arnaldi
Isabelle Arnulf
Emmanuel During
Birgit Högl
Michele M. T. Hu
Alex Iranzo
Russell Luke
John Peever
Ronald B. Postuma
Aleksandar Videnovic
Ziv Gan-Or
From mechanisms to future therapy: a synopsis of isolated REM sleep behavior disorder as early synuclein-related disease
Molecular Neurodegeneration
title From mechanisms to future therapy: a synopsis of isolated REM sleep behavior disorder as early synuclein-related disease
title_full From mechanisms to future therapy: a synopsis of isolated REM sleep behavior disorder as early synuclein-related disease
title_fullStr From mechanisms to future therapy: a synopsis of isolated REM sleep behavior disorder as early synuclein-related disease
title_full_unstemmed From mechanisms to future therapy: a synopsis of isolated REM sleep behavior disorder as early synuclein-related disease
title_short From mechanisms to future therapy: a synopsis of isolated REM sleep behavior disorder as early synuclein-related disease
title_sort from mechanisms to future therapy a synopsis of isolated rem sleep behavior disorder as early synuclein related disease
url https://doi.org/10.1186/s13024-025-00809-0
work_keys_str_mv AT ambrastefani frommechanismstofuturetherapyasynopsisofisolatedremsleepbehaviordisorderasearlysynucleinrelateddisease
AT elenaantelmi frommechanismstofuturetherapyasynopsisofisolatedremsleepbehaviordisorderasearlysynucleinrelateddisease
AT darioarnaldi frommechanismstofuturetherapyasynopsisofisolatedremsleepbehaviordisorderasearlysynucleinrelateddisease
AT isabellearnulf frommechanismstofuturetherapyasynopsisofisolatedremsleepbehaviordisorderasearlysynucleinrelateddisease
AT emmanuelduring frommechanismstofuturetherapyasynopsisofisolatedremsleepbehaviordisorderasearlysynucleinrelateddisease
AT birgithogl frommechanismstofuturetherapyasynopsisofisolatedremsleepbehaviordisorderasearlysynucleinrelateddisease
AT michelemthu frommechanismstofuturetherapyasynopsisofisolatedremsleepbehaviordisorderasearlysynucleinrelateddisease
AT alexiranzo frommechanismstofuturetherapyasynopsisofisolatedremsleepbehaviordisorderasearlysynucleinrelateddisease
AT russellluke frommechanismstofuturetherapyasynopsisofisolatedremsleepbehaviordisorderasearlysynucleinrelateddisease
AT johnpeever frommechanismstofuturetherapyasynopsisofisolatedremsleepbehaviordisorderasearlysynucleinrelateddisease
AT ronaldbpostuma frommechanismstofuturetherapyasynopsisofisolatedremsleepbehaviordisorderasearlysynucleinrelateddisease
AT aleksandarvidenovic frommechanismstofuturetherapyasynopsisofisolatedremsleepbehaviordisorderasearlysynucleinrelateddisease
AT zivganor frommechanismstofuturetherapyasynopsisofisolatedremsleepbehaviordisorderasearlysynucleinrelateddisease