Impact of Central Event Adjudication on the PLATO Trial Results

Background: This study aimed to determine the impact of central adjudication of site-reported events in patients with acute coronary syndromes treated with ticagrelor or clopidogrel in addition to aspirin within the frame of indication-seeking The PLATelet Inhibition and Clinical...

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Main Authors: Victor L. Serebruany, Wendy Ziai, Hector A. Cabrera-Fuentes, Brendon Pokov, Isabella Hwang, Thomas Marciniak
Format: Article
Language:English
Published: IMR Press 2025-04-01
Series:Reviews in Cardiovascular Medicine
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Online Access:https://www.imrpress.com/journal/RCM/26/4/10.31083/RCM36733
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author Victor L. Serebruany
Wendy Ziai
Hector A. Cabrera-Fuentes
Brendon Pokov
Isabella Hwang
Thomas Marciniak
author_facet Victor L. Serebruany
Wendy Ziai
Hector A. Cabrera-Fuentes
Brendon Pokov
Isabella Hwang
Thomas Marciniak
author_sort Victor L. Serebruany
collection DOAJ
description Background: This study aimed to determine the impact of central adjudication of site-reported events in patients with acute coronary syndromes treated with ticagrelor or clopidogrel in addition to aspirin within the frame of indication-seeking The PLATelet Inhibition and Clinical Outcomes (PLATO) trial. Adjudication in randomized outcome-driven trials is supposed to maintain integrity by applying uniform rules for the quality assessment of clinical events. Some preliminary data suggest an imbalance between central and site diagnoses in PLATO. We gained access to the Food and Drug Administration (FDA)-issued adjudication dataset and analyzed the evidence. Methods: Death, myocardial infarction (MI), stroke/ transient ischemic attack (TIA), bleeding, arterial thrombotic events, and cardiac ischemic events underwent central adjudication. We assessed geography, timing, impact of disagreements, and primary endpoint composition. Results: Among 18,624 trial enrollees, 10,704 central adjudications occurred across 7171 patients in 43 countries. There were 938 deaths, 2751 cases of MI, 359 strokes/TIAs, 2680 cardiac events, 130 thrombotic events, and 3782 bleeding events. The match occurred for 5451 events, while mismatches favoring clopidogrel (n = 2535) or ticagrelor (n = 2706) (p = 0.79) were common for major (n = 1797), moderate (n = 942), or minor (n = 735) disagreements. The central decision prevailed in 2945 cases. There was a significant (HR = 0.84; 95% confidence intervals (CI): 0.75–0.95; p = 0.004) adjudication delay in the 2007–2008 events but finalized in 2009. Ticagrelor was significantly less favored in 2009 than in 2007–2008 (HR = 1.19; 95% CI: 1.05–1.34; p = 0.005). There was a remarkably consistent match for bleeding adjudication (HR = 1.02; 95% CI: 0.83–1.25; p = 0.859) between treatment arms. The primary endpoint in the PLATO trial exhibited highly significant disagreement favoring ticagrelor for vascular death (HR = 2.02; 95% CI: 1.1–3.64; p = 0.019); MI (HR = 2.31; 95% CI: 2.79–43.94; p = 0.034); stroke (HR = 1.37; 95% CI: 2.66–63.28; p = 0.036); total events (HR = 2.51; 95% CI: 1.86–3.39; p = 0.01). Conclusion: Central adjudication in the PLATO trial was delayed and impacted the primary endpoint by inflating the ticagrelor benefit, resulting in drug approval. The regulatory authorities should consider independent audits when unblinding is suspected in the indication-seeking clinical trials.
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spelling doaj-art-4e9631c0015543d3aa5b66dc7dfdab202025-08-20T01:48:21ZengIMR PressReviews in Cardiovascular Medicine1530-65502025-04-012643673310.31083/RCM36733S1530-6550(25)01789-2Impact of Central Event Adjudication on the PLATO Trial ResultsVictor L. Serebruany0Wendy Ziai1Hector A. Cabrera-Fuentes2Brendon Pokov3Isabella Hwang4Thomas Marciniak5Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, MD 21205, USADepartment of Neurology, Johns Hopkins University School of Medicine, Baltimore, MD 21205, USAR&D Group, Vice Presidency for Scientific Research and Innovation, Imam Abdulrahman bin Faisal University (IAU), 31441 Dammam, Saudi ArabiaHeartDrug Research LLC, West Friendship, MD 21294, USAHeartDrug Research LLC, West Friendship, MD 21294, USAPhysician, retired from FDA, Alexandria, VA 22314, USABackground: This study aimed to determine the impact of central adjudication of site-reported events in patients with acute coronary syndromes treated with ticagrelor or clopidogrel in addition to aspirin within the frame of indication-seeking The PLATelet Inhibition and Clinical Outcomes (PLATO) trial. Adjudication in randomized outcome-driven trials is supposed to maintain integrity by applying uniform rules for the quality assessment of clinical events. Some preliminary data suggest an imbalance between central and site diagnoses in PLATO. We gained access to the Food and Drug Administration (FDA)-issued adjudication dataset and analyzed the evidence. Methods: Death, myocardial infarction (MI), stroke/ transient ischemic attack (TIA), bleeding, arterial thrombotic events, and cardiac ischemic events underwent central adjudication. We assessed geography, timing, impact of disagreements, and primary endpoint composition. Results: Among 18,624 trial enrollees, 10,704 central adjudications occurred across 7171 patients in 43 countries. There were 938 deaths, 2751 cases of MI, 359 strokes/TIAs, 2680 cardiac events, 130 thrombotic events, and 3782 bleeding events. The match occurred for 5451 events, while mismatches favoring clopidogrel (n = 2535) or ticagrelor (n = 2706) (p = 0.79) were common for major (n = 1797), moderate (n = 942), or minor (n = 735) disagreements. The central decision prevailed in 2945 cases. There was a significant (HR = 0.84; 95% confidence intervals (CI): 0.75–0.95; p = 0.004) adjudication delay in the 2007–2008 events but finalized in 2009. Ticagrelor was significantly less favored in 2009 than in 2007–2008 (HR = 1.19; 95% CI: 1.05–1.34; p = 0.005). There was a remarkably consistent match for bleeding adjudication (HR = 1.02; 95% CI: 0.83–1.25; p = 0.859) between treatment arms. The primary endpoint in the PLATO trial exhibited highly significant disagreement favoring ticagrelor for vascular death (HR = 2.02; 95% CI: 1.1–3.64; p = 0.019); MI (HR = 2.31; 95% CI: 2.79–43.94; p = 0.034); stroke (HR = 1.37; 95% CI: 2.66–63.28; p = 0.036); total events (HR = 2.51; 95% CI: 1.86–3.39; p = 0.01). Conclusion: Central adjudication in the PLATO trial was delayed and impacted the primary endpoint by inflating the ticagrelor benefit, resulting in drug approval. The regulatory authorities should consider independent audits when unblinding is suspected in the indication-seeking clinical trials.https://www.imrpress.com/journal/RCM/26/4/10.31083/RCM36733event adjudicationclinical trialprimary endpointbleedingdeathmyocardial infarctionstroke
spellingShingle Victor L. Serebruany
Wendy Ziai
Hector A. Cabrera-Fuentes
Brendon Pokov
Isabella Hwang
Thomas Marciniak
Impact of Central Event Adjudication on the PLATO Trial Results
Reviews in Cardiovascular Medicine
event adjudication
clinical trial
primary endpoint
bleeding
death
myocardial infarction
stroke
title Impact of Central Event Adjudication on the PLATO Trial Results
title_full Impact of Central Event Adjudication on the PLATO Trial Results
title_fullStr Impact of Central Event Adjudication on the PLATO Trial Results
title_full_unstemmed Impact of Central Event Adjudication on the PLATO Trial Results
title_short Impact of Central Event Adjudication on the PLATO Trial Results
title_sort impact of central event adjudication on the plato trial results
topic event adjudication
clinical trial
primary endpoint
bleeding
death
myocardial infarction
stroke
url https://www.imrpress.com/journal/RCM/26/4/10.31083/RCM36733
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