Stability of symptom-based subtypes in Sjogren’s disease

Objectives The Newcastle Sjogren’s Stratification Tool (NSST) stratifies Sjogren’s disease patients into four subtypes. Understanding the stability of the subtypes is vital if symptom-based stratification is to be more broadly adopted. In this study, we stratify patients longitudinally to understand...

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Main Authors: Xavier Mariette, Jacques-Eric Gottenberg, Jessica Tarn, Wan-Fai Ng, Dennis Lendrem, John Casement, Joe Scott Berry, Kyle Thompson
Format: Article
Language:English
Published: BMJ Publishing Group 2024-11-01
Series:RMD Open
Online Access:https://rmdopen.bmj.com/content/10/4/e004914.full
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author Xavier Mariette
Jacques-Eric Gottenberg
Jessica Tarn
Wan-Fai Ng
Dennis Lendrem
John Casement
Joe Scott Berry
Kyle Thompson
author_facet Xavier Mariette
Jacques-Eric Gottenberg
Jessica Tarn
Wan-Fai Ng
Dennis Lendrem
John Casement
Joe Scott Berry
Kyle Thompson
author_sort Xavier Mariette
collection DOAJ
description Objectives The Newcastle Sjogren’s Stratification Tool (NSST) stratifies Sjogren’s disease patients into four subtypes. Understanding the stability of the subtypes is vital if symptom-based stratification is to be more broadly adopted. In this study, we stratify patients longitudinally to understand how symptom-based subtypes vary over time and factors influencing subtype change.Methods 274 patients from the United Kingdom Primary Sjögren’s Syndrome Registry (UKPSSR) with data permitting NSST subtype assignment from two study visits were included. The French Assessment of Systemic Signs and Evolution of Sjogren’s Syndrome (ASSESS) cohort (n=237) acted as an independent comparator. Group analyses of significant differences were performed, with logistic regression models used to assess covariates of subtype stability.Results UKPSSR and ASSESS cohorts showed a broadly similar proportion of subjects in each subtype and similar baseline clinical characteristics except body mass index (BMI). Several baseline characteristics differ significantly between the subtypes, most notably anti-Ro status and BMI. Subtype membership was reasonably stable in both cohorts with 60% and 57% retaining subtype. The high-symptom burden subtype was the most stable over time with 70% and 67% retaining subtype. Higher baseline probability score was the greatest predictor of subtype stability with higher C4 levels, antidepressant use, and a higher CCI score also predicting increased stability.Conclusion NSST subtype membership remains stable over time in a large proportion of patients. When subtype transition is associated with factors at baseline, it is most strongly associated with an uncertain subtype allocation. Our findings support the hypothesis that symptom-based subtypes reflect genuine pathobiological endotypes and therefore maybe important to consider in trial design and clinical management.
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spelling doaj-art-4e2ecbca06d348b48bf9f56adeff6b442025-08-20T02:32:20ZengBMJ Publishing GroupRMD Open2056-59332024-11-0110410.1136/rmdopen-2024-004914Stability of symptom-based subtypes in Sjogren’s diseaseXavier Mariette0Jacques-Eric Gottenberg1Jessica Tarn2Wan-Fai Ng3Dennis Lendrem4John Casement5Joe Scott Berry6Kyle Thompson7Rhumatology Department, Centre Hospitalier Universitaire Bicêtre, Le Kremlin-Bicêtre, France27 Strasbourg University Hospital and University of Strasbourg, CNRS, Institut de Biologie Moléculaire et Cellulaire, Immunopathologie, et Chimie Thérapeutique, Strasbourg, France1Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, Tyne and Wear, UKTranslational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, UK1Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, Tyne and Wear, UKBioinformatics Support Unit, Newcastle University, Newcastle upon Tyne, UK1Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, Tyne and Wear, UK1Translational and Clinical Research Institute, Newcastle University, Newcastle upon Tyne, Tyne and Wear, UKObjectives The Newcastle Sjogren’s Stratification Tool (NSST) stratifies Sjogren’s disease patients into four subtypes. Understanding the stability of the subtypes is vital if symptom-based stratification is to be more broadly adopted. In this study, we stratify patients longitudinally to understand how symptom-based subtypes vary over time and factors influencing subtype change.Methods 274 patients from the United Kingdom Primary Sjögren’s Syndrome Registry (UKPSSR) with data permitting NSST subtype assignment from two study visits were included. The French Assessment of Systemic Signs and Evolution of Sjogren’s Syndrome (ASSESS) cohort (n=237) acted as an independent comparator. Group analyses of significant differences were performed, with logistic regression models used to assess covariates of subtype stability.Results UKPSSR and ASSESS cohorts showed a broadly similar proportion of subjects in each subtype and similar baseline clinical characteristics except body mass index (BMI). Several baseline characteristics differ significantly between the subtypes, most notably anti-Ro status and BMI. Subtype membership was reasonably stable in both cohorts with 60% and 57% retaining subtype. The high-symptom burden subtype was the most stable over time with 70% and 67% retaining subtype. Higher baseline probability score was the greatest predictor of subtype stability with higher C4 levels, antidepressant use, and a higher CCI score also predicting increased stability.Conclusion NSST subtype membership remains stable over time in a large proportion of patients. When subtype transition is associated with factors at baseline, it is most strongly associated with an uncertain subtype allocation. Our findings support the hypothesis that symptom-based subtypes reflect genuine pathobiological endotypes and therefore maybe important to consider in trial design and clinical management.https://rmdopen.bmj.com/content/10/4/e004914.full
spellingShingle Xavier Mariette
Jacques-Eric Gottenberg
Jessica Tarn
Wan-Fai Ng
Dennis Lendrem
John Casement
Joe Scott Berry
Kyle Thompson
Stability of symptom-based subtypes in Sjogren’s disease
RMD Open
title Stability of symptom-based subtypes in Sjogren’s disease
title_full Stability of symptom-based subtypes in Sjogren’s disease
title_fullStr Stability of symptom-based subtypes in Sjogren’s disease
title_full_unstemmed Stability of symptom-based subtypes in Sjogren’s disease
title_short Stability of symptom-based subtypes in Sjogren’s disease
title_sort stability of symptom based subtypes in sjogren s disease
url https://rmdopen.bmj.com/content/10/4/e004914.full
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