X-linked Thrombocytopenia with Normal Wiskott-Aldrich Syndrome Protein Expression in Lymphocytes and a Novel Wiskott-Aldrich Syndrome Protein Gene Variant: A Case Report and Brief Review of the Literature

We present a case of X-linked thrombocytopenia (XLT) with a novel WAS gene variant expressing a normal amount of Wiskott-Aldrich syndrome protein (WASp) in lymphocytes. XLT usually decreases WASp expression not only in platelets, but also in lymphocytes. However, there were cases, such as the presen...

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Main Authors: Serena Hamanaka, MD, Toru Uchiyama, MD, PhD, Tadashi Kaname, MD, PhD, Motohiro Matsui, MD, Hiroshi Yoshihashi, MD, Atsushi Makimoto, MD, PhD, Yuki Yuza, MD, Akira Ishiguro, MD
Format: Article
Language:English
Published: Elsevier 2024-12-01
Series:Journal of Pediatrics: Clinical Practice
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Online Access:http://www.sciencedirect.com/science/article/pii/S2950541024000346
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author Serena Hamanaka, MD
Toru Uchiyama, MD, PhD
Tadashi Kaname, MD, PhD
Motohiro Matsui, MD
Hiroshi Yoshihashi, MD
Atsushi Makimoto, MD, PhD
Yuki Yuza, MD
Akira Ishiguro, MD
author_facet Serena Hamanaka, MD
Toru Uchiyama, MD, PhD
Tadashi Kaname, MD, PhD
Motohiro Matsui, MD
Hiroshi Yoshihashi, MD
Atsushi Makimoto, MD, PhD
Yuki Yuza, MD
Akira Ishiguro, MD
author_sort Serena Hamanaka, MD
collection DOAJ
description We present a case of X-linked thrombocytopenia (XLT) with a novel WAS gene variant expressing a normal amount of Wiskott-Aldrich syndrome protein (WASp) in lymphocytes. XLT usually decreases WASp expression not only in platelets, but also in lymphocytes. However, there were cases, such as the present one, in which WASp was expressed normally in lymphocytes and absent only in platelets. Our finding suggests that it is of greater diagnostic sensitivity to perform an expression analysis of WASp in both platelets and lymphocytes when XLT is suspected.
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id doaj-art-3dafd6dba22f46859e9e68ef6f1112e6
institution OA Journals
issn 2950-5410
language English
publishDate 2024-12-01
publisher Elsevier
record_format Article
series Journal of Pediatrics: Clinical Practice
spelling doaj-art-3dafd6dba22f46859e9e68ef6f1112e62025-08-20T02:35:50ZengElsevierJournal of Pediatrics: Clinical Practice2950-54102024-12-011420012810.1016/j.jpedcp.2024.200128X-linked Thrombocytopenia with Normal Wiskott-Aldrich Syndrome Protein Expression in Lymphocytes and a Novel Wiskott-Aldrich Syndrome Protein Gene Variant: A Case Report and Brief Review of the LiteratureSerena Hamanaka, MD0Toru Uchiyama, MD, PhD1Tadashi Kaname, MD, PhD2Motohiro Matsui, MD3Hiroshi Yoshihashi, MD4Atsushi Makimoto, MD, PhD5Yuki Yuza, MD6Akira Ishiguro, MD7Department of General Pediatrics, Tokyo Metropolitan Children's Medical Center, Tokyo, Japan; Reprint requests: Serena Hamanaka, MD, Department of General Pediatrics, Tokyo Metropolitan Children's Medical Center, 2-8-29 Musashidai, Fuchu, Tokyo 183-8561, Japan.Department of Human Genetics, National Center for Child Health and Development, Tokyo, JapanDepartment of Genome Medicine, National Center for Child Health and Development, Tokyo, JapanDepartment of Hematology/Oncology, Tokyo Metropolitan Children's Medical Center, Tokyo, JapanDepartment of Clinical Genetics, Tokyo Metropolitan Children's Medical Center, Tokyo, JapanDepartment of Hematology/Oncology, Tokyo Metropolitan Children's Medical Center, Tokyo, JapanDepartment of Hematology/Oncology, Tokyo Metropolitan Children's Medical Center, Tokyo, JapanCenter for Postgraduate Education and Training, National Center for Child Health and Development, Tokyo, JapanWe present a case of X-linked thrombocytopenia (XLT) with a novel WAS gene variant expressing a normal amount of Wiskott-Aldrich syndrome protein (WASp) in lymphocytes. XLT usually decreases WASp expression not only in platelets, but also in lymphocytes. However, there were cases, such as the present one, in which WASp was expressed normally in lymphocytes and absent only in platelets. Our finding suggests that it is of greater diagnostic sensitivity to perform an expression analysis of WASp in both platelets and lymphocytes when XLT is suspected.http://www.sciencedirect.com/science/article/pii/S2950541024000346X-linked thrombocytopeniaWiskott-Aldrich syndrome proteinnovel variantlymphocyte
spellingShingle Serena Hamanaka, MD
Toru Uchiyama, MD, PhD
Tadashi Kaname, MD, PhD
Motohiro Matsui, MD
Hiroshi Yoshihashi, MD
Atsushi Makimoto, MD, PhD
Yuki Yuza, MD
Akira Ishiguro, MD
X-linked Thrombocytopenia with Normal Wiskott-Aldrich Syndrome Protein Expression in Lymphocytes and a Novel Wiskott-Aldrich Syndrome Protein Gene Variant: A Case Report and Brief Review of the Literature
Journal of Pediatrics: Clinical Practice
X-linked thrombocytopenia
Wiskott-Aldrich syndrome protein
novel variant
lymphocyte
title X-linked Thrombocytopenia with Normal Wiskott-Aldrich Syndrome Protein Expression in Lymphocytes and a Novel Wiskott-Aldrich Syndrome Protein Gene Variant: A Case Report and Brief Review of the Literature
title_full X-linked Thrombocytopenia with Normal Wiskott-Aldrich Syndrome Protein Expression in Lymphocytes and a Novel Wiskott-Aldrich Syndrome Protein Gene Variant: A Case Report and Brief Review of the Literature
title_fullStr X-linked Thrombocytopenia with Normal Wiskott-Aldrich Syndrome Protein Expression in Lymphocytes and a Novel Wiskott-Aldrich Syndrome Protein Gene Variant: A Case Report and Brief Review of the Literature
title_full_unstemmed X-linked Thrombocytopenia with Normal Wiskott-Aldrich Syndrome Protein Expression in Lymphocytes and a Novel Wiskott-Aldrich Syndrome Protein Gene Variant: A Case Report and Brief Review of the Literature
title_short X-linked Thrombocytopenia with Normal Wiskott-Aldrich Syndrome Protein Expression in Lymphocytes and a Novel Wiskott-Aldrich Syndrome Protein Gene Variant: A Case Report and Brief Review of the Literature
title_sort x linked thrombocytopenia with normal wiskott aldrich syndrome protein expression in lymphocytes and a novel wiskott aldrich syndrome protein gene variant a case report and brief review of the literature
topic X-linked thrombocytopenia
Wiskott-Aldrich syndrome protein
novel variant
lymphocyte
url http://www.sciencedirect.com/science/article/pii/S2950541024000346
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