The human ABCG2 transporter engages three gates to control multidrug extrusion

Summary: The human ABCG2 transporter plays roles in physiological detoxification across barriers and in anticancer multidrug resistance. The translocation pathway for drug extrusion and its gating mechanism remains elusive. Here, we demonstrate that the ABCG2 multidrug transporter holds two cavities...

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Main Authors: Narakorn Khunweeraphong, Karl Kuchler
Format: Article
Language:English
Published: Elsevier 2025-03-01
Series:iScience
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Online Access:http://www.sciencedirect.com/science/article/pii/S2589004225003852
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author Narakorn Khunweeraphong
Karl Kuchler
author_facet Narakorn Khunweeraphong
Karl Kuchler
author_sort Narakorn Khunweeraphong
collection DOAJ
description Summary: The human ABCG2 transporter plays roles in physiological detoxification across barriers and in anticancer multidrug resistance. The translocation pathway for drug extrusion and its gating mechanism remains elusive. Here, we demonstrate that the ABCG2 multidrug transporter holds two cavities that are delineated by three regulatory gates, indicating a substrate translocation channel. Drugs are trapped in the central cavity after entering through the pivotal intracellular entry gate. This flexible cavity is surrounded by a cluster of three highly conserved phenylalanines. Their aromatic side chains enact a “clamp-push-seal” motion to ensure unidirectional substrate movement. The unique residues T435 and N436 act as critical selectors for ligands, determining the broad substrate specificity. The upper cavity is covered by the lid architecture, constituting the final gate before multidrug extrusion. This work unravels deep mechanistic details on how the translocation channel utilizes pivotal gating steps, including the sequence of events that drive ABCG2-mediated multidrug efflux.
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spelling doaj-art-0775c11b33014f16af9c62afd78b98412025-08-20T02:55:54ZengElsevieriScience2589-00422025-03-0128311212510.1016/j.isci.2025.112125The human ABCG2 transporter engages three gates to control multidrug extrusionNarakorn Khunweeraphong0Karl Kuchler1Medical University of Vienna, Max Perutz Labs Vienna, Center for Medical Biochemistry Campus Vienna Biocenter, Dr. Bohr-Gasse 9/2, 1030 Vienna, AustriaMedical University of Vienna, Max Perutz Labs Vienna, Center for Medical Biochemistry Campus Vienna Biocenter, Dr. Bohr-Gasse 9/2, 1030 Vienna, Austria; Corresponding authorSummary: The human ABCG2 transporter plays roles in physiological detoxification across barriers and in anticancer multidrug resistance. The translocation pathway for drug extrusion and its gating mechanism remains elusive. Here, we demonstrate that the ABCG2 multidrug transporter holds two cavities that are delineated by three regulatory gates, indicating a substrate translocation channel. Drugs are trapped in the central cavity after entering through the pivotal intracellular entry gate. This flexible cavity is surrounded by a cluster of three highly conserved phenylalanines. Their aromatic side chains enact a “clamp-push-seal” motion to ensure unidirectional substrate movement. The unique residues T435 and N436 act as critical selectors for ligands, determining the broad substrate specificity. The upper cavity is covered by the lid architecture, constituting the final gate before multidrug extrusion. This work unravels deep mechanistic details on how the translocation channel utilizes pivotal gating steps, including the sequence of events that drive ABCG2-mediated multidrug efflux.http://www.sciencedirect.com/science/article/pii/S2589004225003852Natural sciencesBiological sciencesBiochemistryMicrobiologyMolecular microbiology
spellingShingle Narakorn Khunweeraphong
Karl Kuchler
The human ABCG2 transporter engages three gates to control multidrug extrusion
iScience
Natural sciences
Biological sciences
Biochemistry
Microbiology
Molecular microbiology
title The human ABCG2 transporter engages three gates to control multidrug extrusion
title_full The human ABCG2 transporter engages three gates to control multidrug extrusion
title_fullStr The human ABCG2 transporter engages three gates to control multidrug extrusion
title_full_unstemmed The human ABCG2 transporter engages three gates to control multidrug extrusion
title_short The human ABCG2 transporter engages three gates to control multidrug extrusion
title_sort human abcg2 transporter engages three gates to control multidrug extrusion
topic Natural sciences
Biological sciences
Biochemistry
Microbiology
Molecular microbiology
url http://www.sciencedirect.com/science/article/pii/S2589004225003852
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