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Switching to subcutaneous zilucoplan from intravenous complement component 5 inhibitors in generalised myasthenia gravis: a phase IIIb, open-label study by Miriam Freimer, Urvi Desai, Raghav Govindarajan, Min K. Kang, Shaida Khan, Bhupendra Khatri, Todd Levine, Samir Macwan, Perry B. Shieh, Michael D. Weiss, Jos Bloemers, Babak Boroojerdi, Eumorphia Maria Delicha, Andreea Lavrov, Puneet Singh, James F. Howard
Published 2025-07-01Get full text
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Prospective observational study of FKRP‐related limb‐girdle muscular dystrophy R9: A GRASP consortium study by Lindsay N. Alfano, Meredith K. James, Kristine Grosfjeld Petersen, Karen Rudolf, John Vissing, Renee Augsburger, Tahseen Mozaffar, Aileen Jones, Amanda Butler, Katie M. Laubscher, Shelley R. H. Mockler, Katherine D. Mathews, Megan A. Iammarino, Natalie F. Reash, Lindsay Pietruszewski, Linda P. Lowes, Talia Strahler, Matthew Wicklund, Stephanie Hunn, Conrad C. Weihl, Sandhya Sasidharan, Melissa Currence, Jeffrey M. Statland, Nikia Stinson, Megan Holzer, Doris G. Leung, Donovan J. Lott, Peter B. Kang, Scott Holsten, Urvi Desai, Nicholas E. Johnson, the GRASP‐LGMD Consortium
Published 2025-02-01Get full text
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