BCL11A-deficient human erythropoiesis is impaired in vitro and after xenotransplantation into mice by Yoonjeong Jang, Ruopeng Feng, Lance E. Palmer, Thiyagaraj Mayuranathan, Yu Yao, Kalin Mayberry, Sheng Zhou, Jian Xu, Jeffrey M. Gossett, Guolian Kang, Yong Cheng, Jonathan S. Yen, Mitchell J. Weiss

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Removal of promoter CpG methylation by epigenome editing reverses HBG silencing by Henry W. Bell, Ruopeng Feng, Manan Shah, Yu Yao, James Douglas, Phillip A. Doerfler, Thiyagaraj Mayuranathan, Michael F. O’Dea, Yichao Li, Yong-Dong Wang, Jingjing Zhang, Joel P. Mackay, Yong Cheng, Kate G. R. Quinlan, Mitchell J. Weiss, Merlin Crossley

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Multiplex base editing to protect from CD33 directed drugs for immune and gene therapy by Florence Borot, Olivier Humbert, Jeffrey T. Ehmsen, Emily Fields, Sajeev Kohli, Stefan Radtke, Kyle Swing, Dnyanada Pande, Mark R. Enstrom, George S. Laszlo, Thiyagaraj Mayuranathan, Abdullah Mahmood Ali, Mitchell J. Weiss, Jonathan S. Yen, Gregory A. Newby, Roland B. Walter, David R. Liu, Siddhartha Mukherjee, Hans-Peter Kiem

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