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N-glycan-modified α-L-iduronidase produced by transgenic silkworms ameliorates clinical signs in a Japanese macaque with mucopolysaccharidosis I by Chika Shinoda, Keisuke Kitakaze, Yuya Sasai, So-Ichiro Nishioka, Isao Kobayashi, Megumi Sumitani, Ken-Ichiro Tatematsu, Tetsuya Iizuka, Akira Harazono, Ai Mitani, Akihisa Kaneko, Masanori Imamura, Takako Miyabe-Nishiwaki, Yasuhiro Go, Akihiro Hirata, Yoshie Takeuchi, Teru Mizuno, Kei Kiriyama, Jun Tsukimoto, Satomi Nadanaka, Akiko Ishii-Watabe, Takashi Kinoshita, Hiroshi Kitagawa, Yasuyuki Suzuki, Takao Oishi, Hideki Sezutsu, Kohji Itoh
Published 2025-04-01Get full text
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