Showing 1 - 2 results of 2 for search 'Stephanie Grunewald', query time: 0.01s Refine Results
  1. 1
    P008: A first in human, single arm, open label phase 1/2 study evaluating ECUR-506 in neonatal OTC Deficiency: Initial Observations

    P008: A first in human, single arm, open label phase 1/2 study evaluating ECUR-506 in neonatal OTC Deficiency: Initial Observations by Julien Baruteau, Gabriel Cohn, Anil Dhawan, Anupam Chakrapani, Stephanie Grunewald, Molly Abbott, Helen Ashton, Sophie Foxall, Ai Ling Koh, Christos Lazaridis, Havea Navarro-Kennedy, Hamza Patel, Siyamini Sivananthan, Eleni Tamvaki, Katy Vecchiato, Matthew Hall, Karen Kuhn, Thomas White, Barbara Pinho, George Diaz

    Published 2025-01-01
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  2. 2
    Efficacy results from a 12-month double-blind randomized trial of arimoclomol for treatment of Niemann-Pick disease type C (NPC): Presenting a rescored 4-domain NPC Clinical Severity Scale

    Efficacy results from a 12-month double-blind randomized trial of arimoclomol for treatment of Niemann-Pick disease type C (NPC): Presenting a rescored 4-domain NPC Clinical Severi... by Eugen Mengel, Marc C. Patterson, Rosalia M. Da Riol, Mireia Del Toro, Federica Deodato, Matthias Gautschi, Stephanie Grunewald, Sabine Weller Grønborg, Paul Harmatz, Julia B. Hennermann, Bénédicte Héron, Esther M. Maier, Agathe Roubertie, Saikat Santra, Anna Tylki-Szymanska, Lisa LaGorio, Elizabeth Berry-Kravis, Forbes D. Porter, Beth Solomon, Louise Himmelstrup, Travis Mickle, Sven Guenther, Christine í Dali

    Published 2025-06-01
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