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Neonatal neuronal WWOX gene therapy rescues Wwox null phenotypes by Srinivasarao Repudi, Irina Kustanovich, Sara Abu‐Swai, Shani Stern, Rami I Aqeilan
Published 2021-11-01Get full text
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Generation of human induced pluripotent stem cell lines HUJIi004 and HUJIi005 from two individuals carrying autosomal-dominant mutations in the CTNBB1 gene resulting in CTNNB1 neur... by Daniel J. Steinberg, Kian Maroun, Srinivasarao Repudi, Bruria Ben-Zeev, Rami I. Aqeilan
Published 2025-03-01Get full text
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Modeling genetic epileptic encephalopathies using brain organoids by Daniel J Steinberg, Srinivasarao Repudi, Afifa Saleem, Irina Kustanovich, Sergey Viukov, Baraa Abudiab, Ehud Banne, Muhammad Mahajnah, Jacob H Hanna, Shani Stern, Peter L Carlen, Rami I Aqeilan
Published 2021-07-01Get full text
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