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Lysosomal free sialic acid storage disorder iPSC-derived neural cells display altered glycosphingolipid metabolism by Marya S. Sabir, Vukasin M. Jovanovic, Seungmi Ryu, Chaitali Sen, Pinar Ormanoglu, Laura Pollard, Richard Steet, William A. Gahl, Marjan Huizing, Carlos A. Tristan, Frances M. Platt, May Christine V. Malicdan
Published 2025-08-01Get full text
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