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Evaluating the feasibility of gene replacement strategies to treat MTRFR deficiency by Samia L. Pratt, Mariana Zarate-Mendez, Lidiia Koludarova, Sonja Jansson, Mikko Airavaara, Irena Hlushchuk, David Coleman, Caleb Heffner, Rita Horvath, Brendan J. Battersby, Robert W. Burgess
Published 2025-05-01Get full text
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