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Efficacy and preliminary safety assessment of EXG001-307 AAV gene therapy for spinal muscular atrophy by Chunjuan Song, Qingzeng Wang, Peixin Zhu, Junhui Li, Li Dai, Wei Hu, Wenshu Yang, Runyuan Zhang, Dandan Wang, Zhongwan Li, Shuyuan Chen, Lijun Wang, Guojie Ye, Zhenhua Wu
Published 2025-06-01Get full text
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