Showing 1 - 2 results of 2 for search 'Rebecca Ahrens-Nicklas' Skip to content
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  • Rebecca Ahrens-Nicklas
Showing 1 - 2 results of 2 for search 'Rebecca Ahrens-Nicklas', query time: 0.02s Refine Results
  1. 1
    Bone marrow transplantation reverses metabolic alterations in multiple sulfatase deficiency: a case series

    Bone marrow transplantation reverses metabolic alterations in multiple sulfatase deficiency: a case series by Nishitha R. Pillai, Ning Liu, Xiyuan Li, Xiqi Li, Rebecca Ahrens-Nicklas, Laura Adang, Julie B. Eisengart, Grace Bronken, Ashish Gupta, Troy C. Lund, Chester B. Whitley, Sarah H. Elsea, Paul J. Orchard

    Published 2025-01-01
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  2. 2
    Pantethine ameliorates dilated cardiomyopathy features in PPCS deficiency disorder in patients and cell line models

    Pantethine ameliorates dilated cardiomyopathy features in PPCS deficiency disorder in patients and cell line models by Fangfang Zhang, Tatjana Dorn, Barbara Gnutti, Yair Anikster, Sarah Kuebler, Rebecca Ahrens-Nicklas, Rachel Gosselin, Shamima Rahman, Ronen Durst, Enrica Zanuttigh, Miriam A. Güra, Christine M. Poch, Anna B. Meier, Karl-Ludwig Laugwitz, Hans-Joachim Schüller, Ana C. Messias, Ody C. Sibon, Dario Finazzi, Alyssa Rippert, Dong Li, Kristen Truxal, Deipanjan Nandi, Brent C. Lampert, Mildrid Yeo, Alice Gardham, Batel Nissan, Smadar Horowitz Cederboim, Alessandra Moretti, Arcangela Iuso

    Published 2025-07-01
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