Preclinical ex vivo IL2RG gene therapy using autologous hematopoietic stem cells as an effective and safe treatment for X-linked severe combined immunodeficiency disease by Mingfeng Hu, Qiling Xu, Fang Zhang, Karen F. Buckland, Yelei Gao, Weixia Du, Yuan Ding, Lina Zhou, Xiulian Sun, Lijia Ma, Zhiyong Zhang, Xuemei Tang, Xiaodong Zhao, Adrian J. Thrasher, Yunfei An

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