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Showing 1 - 1 results of 1 for search 'Patrick T. Harrison', query time: 0.01s Refine Results
  1. 1
    Adenine base editing with engineered virus-like particles rescues the CFTR mutation G542X in patient-derived intestinal organoids

    Adenine base editing with engineered virus-like particles rescues the CFTR mutation G542X in patient-derived intestinal organoids by Lucia Nicosia, Iwona Pranke, Roberta V. Latorre, Joss B. Murray, Lisa Lonetti, Kader Cavusoglu-Doran, Elise Dreano, James P. Costello, Michael Carroll, Paola Melotti, Claudio Sorio, Isabelle Sermet-Gaudelus, Martina F. Scallan, Patrick T. Harrison

    Published 2025-03-01
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