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Novel transferrin receptor-mediated enzyme replacement therapy efficiently treats myogenic and neurogenic aspects of Pompe disease in mice by Kelly George, Raquel Riley, Shan Zhou, Elizabeth Allen, Laurie Smith, Elena Kistanova, Sofia Kinton, Lilu Guo, Dinesh Bangari, Ayman Ismail, Jayaprakash Thummapudi, Fawzi Boumezbeur, Erwan Selingue, Dorothée Tamarelle, Cecile Capdevila, Tuan-Minh Do, Dominique Lesuisse, Nina Leksa, Pablo Sardi, Arjan van der Flier
Published 2025-09-01Get full text
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A brain-shuttled antibody targeting alpha synuclein aggregates for the treatment of synucleinopathies by Sungwon An, John J. McInnis, Dongin Kim, Yihang Li, Ozge Tasdemir-Yilmaz, Jinhyung Ahn, Brian C. Mackness, Seung-Hwan Kwon, Julia Maeve Bonner, Miran Yoo, Simon Dujardin, Donghwan Kim, Jinyoung Park, Hyesu Yun, Yi Tang, Laurent Pradier, Sumin Hyeon, Daehae Song, Byungje Sung, Rajaraman Krishnan, Brian Spencer, Robert A. Rissman, Jagdeep K. Sandhu, Arsalan S. Haqqani, Jung-Won Shin, Donghwan B. Kim, Hyeran Lee, Jinwon Jung, Weon-Kyoo You, Alexandra T. Star, Christie E. Delaney, Danica B. Stanimirovic, Sergio Pablo Sardi, Sang Hoon Lee, Can Kayatekin
Published 2025-08-01Get full text
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