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Damoctocog Alfa Pegol, a PEGylated B-domain Deleted Recombinant Extended Half-life Factor VIII for the Treatment of Hemophilia A: A Product Review by Mark T. Reding, Shadan Lalezari, Gili Kenet, Giovanni Di Minno, Jonathan Ducore, Alexander Solms, Anita Shah, Pål André Holme, Lone H. Poulsen, Karina Meijer, Mindy Simpson, Maria Elisa Mancuso
Published 2024-08-01Get full text
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Correction: Damoctocog Alfa Pegol, a PEGylated B-domain Deleted Recombinant Extended Half-life Factor VIII for the Treatment of Hemophilia A: A Product Review by Mark T. Reding, Shadan Lalezari, Gili Kenet, Giovanni Di Minno, Jonathan Ducore, Alexander Solms, Anita Shah, Pål André Holme, Lone H. Poulsen, Karina Meijer, Mindy Simpson, Maria Elisa Mancuso
Published 2024-12-01Get full text
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Inhibitor development and clinical characteristics in children with severe hemophilia A in the ATHN 8 US cohort study by Courtney D. Thornburg, H. Marijke van den Berg, Martin Chandler, Lynn Malec, Matthew Manuel, Carrie O’Neill, Michael Recht, Elizabeth Taggart, Shannon L. Carpenter, Christine Knoll, Lynn Malec, Michael Wang, Michael Guerrera, Cristina Tarango, Robert Sidonio, Nidra Rodriguez, Kenneth D. Friedman, Amy Shapiro, Hassan Yaish, Shannon Carpenter, Maissaa Janbain, Eric Grabowski, Rajiv Pruthi, Kristina Haley, Courtney Thornburg, Sanjay Ahuja, Mindy Simpson, Ulrike Reiss, Tiffany Lucas, Vinod Balasa, Allison Wheeler
Published 2025-08-01Get full text
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Effect of DNA methylation on inhibitor development in people with hemophilia A treated with FVIII concentrates by Himani Chand, Shermarke Hassan, Andrea Cairo, Roberta Palla, Flora Peyvandi, Flora Peyvandi, Pier M. Mannucci, Isabella Garagiola, Amal El-Beshlawy, Mohsen Elalfy, Vijay Ramanan, Peyman Eshghi, Suresh Hanagavadi, Ramabadran Varadarajan, Mehran Karimi, Mamta V. Manglani, Cecil Ross, Guy Young, Tulika Seth, Shashikant Apte, Dinesh M. Nayak, Elena Santagostino, Maria Elisa Mancuso, Adriana C. Sandoval Gonzalez, Johnny N. Mahlangu, Santiago Bonanad Boix, Monica Cerqueira, Nadia P. Ewing, Christoph Male, Tarek Owaidah, Veronica Soto Arellano, Nathan L. Kobrinsky, Suvankar Majumdar, Rosario Perez Garrido, Anupam Sachdeva, Mindy Simpson, Mathew Thomas, Ezio Zanon, Bulent Antmen, Kaan Kavakli, Marilyn J. Manco-Johnson, Monica Martinez, Esperanza Marzouka, Maria G. Mazzucconi, Daniela Neme, Angeles Palomo Bravo, Rogelio Paredes Aguilera, Alessandra Prezotti, Klaus Schmitt, Brian M. Wicklund, Bulent Zulfikar, Frits R. Rosendaal
Published 2025-03-01Get full text
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