Completion of phase 2b trial of etranacogene dezaparvovec gene therapy in patients with hemophilia B over 5 years by Annette von Drygalski, Esteban Gomez, Adam Giermasz, Giancarlo Castaman, Nigel S. Key, Susan U. Lattimore, Frank W. G. Leebeek, Wolfgang A. Miesbach, Michael Recht, Paul E. Monahan, Sandra Le Quellec, Steven W. Pipe

Get full text

Inhibitor development and clinical characteristics in children with severe hemophilia A in the ATHN 8 US cohort study by Courtney D. Thornburg, H. Marijke van den Berg, Martin Chandler, Lynn Malec, Matthew Manuel, Carrie O’Neill, Michael Recht, Elizabeth Taggart, Shannon L. Carpenter, Christine Knoll, Lynn Malec, Michael Wang, Michael Guerrera, Cristina Tarango, Robert Sidonio, Nidra Rodriguez, Kenneth D. Friedman, Amy Shapiro, Hassan Yaish, Shannon Carpenter, Maissaa Janbain, Eric Grabowski, Rajiv Pruthi, Kristina Haley, Courtney Thornburg, Sanjay Ahuja, Mindy Simpson, Ulrike Reiss, Tiffany Lucas, Vinod Balasa, Allison Wheeler

Get full text