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Evaluating treatment and care outcomes for neuromuscular diseases in a pediatric intermediate care setting by Giacomo Brisca, Marina F. Strati, Marina F. Strati, Francesca Canzoneri, Marcello Mariani, Daniela Pirlo, Marta Romanengo, Giacomo Tardini, Noemi Brolatti, Silvia Buratti, Silvia Buratti, Marina Pedemonte, Chiara Fiorillo, Chiara Fiorillo, Pasquale Striano, Pasquale Striano, Claudio Bruno, Claudio Bruno, Andrea Moscatelli
Published 2025-04-01Get full text
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Opinion of the Italian Association of Myology on Ataluren for the Treatment of Nonsense Mutation Duchenne Muscular Dystrophy by Luca Bello, Pietro Riguzzi, Emilio Albamonte, Guja Astrea, Roberta Battini, Andrea Barp, Angela L. Berardinelli, Enrico S. Bertini, Noemi Brolatti, Claudio Bruno, Stefania Corti, Adele D’Amico, Maria Grazia D’Angelo, Gianfranco Dallavalle, Rocco Liguori, Lorenzo Maggi, Francesca Magri, Michelangelo Mancuso, Riccardo Masson, Eugenio Mercuri, Carlo Minetti, Sonia Messina, Tiziana Mongini, Olimpia Musumeci, Vincenzo Nigro, Marika Pane, Chiara Panicucci, Marina Pedemonte, Antonella Pini, Luisa Politano, Stefano Previtali, Federica Ricci, Giulia Ricci, Lucia Ruggiero, Valeria Sansone, Gabriele Siciliano, Antonio Trabacca, Federica Trucco, Daniele Velardo, Elena Pegoraro, Giacomo P. Comi
Published 2025-05-01Get full text
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