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Activated prothrombin complex concentrate in patients receiving emicizumab prophylaxis: from evidence to clinical practice by Robert F. Sidonio, Jr., Guy Young, Carmen Escuriola Ettingshausen, Johnny Mahlangu, Margareth C. Ozelo, Alok Srivastava, Jerzy Windyga, Hye–Youn Lee, Aurelia Lelli, Steven W. Pipe
Published 2025-05-01Get full text
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New insights into Wiskott-Aldrich syndrome: ten novel WAS mutations and their clinical impact in a Brazilian cohort by Lucas W. Santos, Samuel S. Medina, Jéssica O. Frade-Guanaes, Lúcia H. Siqueira, Luiz Gustavo R. de Lima, Luiz Gustavo R. de Lima, Bruna Chati, Bruna Chati, Marcos T. Nolasco da Silva, Marcos T. Nolasco da Silva, Adriana G. L. Riccetto, Adriana G. L. Riccetto, Paula Lyra, Ana Carla A. M. Falcão, Pedro P. A. Santos, Regina S. W. Di Gesu, Bianca Stefanello, Bianca Stefanello, Gabriela G. Yamaguti-Hayakawa, Carmem M. S. Bonfim, Maria M. S. Vilela, Maria M. S. Vilela, Margareth C. Ozelo, Margareth C. Ozelo
Published 2025-07-01Get full text
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Efficacy, safety, and quality of life 4 years after valoctocogene roxaparvovec gene transfer for severe hemophilia A in the phase 3 GENEr8-1 trial by Andrew D. Leavitt, Johnny Mahlangu, Priyanka Raheja, Emily Symington, Doris V. Quon, Adam Giermasz, Maria Fernanda López Fernández, Gili Kenet, Gillian Lowe, Nigel S. Key, Carolyn M. Millar, Steven W. Pipe, Bella Madan, Sheng-Chieh Chou, Robert Klamroth, Jane Mason, Hervé Chambost, Flora Peyvandi, Elaine Majerus, Dominic Pepperell, Christine Rivat, Hua Yu, Tara M. Robinson, Margareth C. Ozelo
Published 2024-11-01Get full text
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