Impact of elexacaftor/tezacaftor/ivacaftor (ETI) on the prescription refill rate (PRR) for inhaled medications in people with CF: an Italian multicenter analysis by Andrea Gramegna, Giuseppe Cimino, Marco Cipolli, Giovanna Gandini, Maria Adelaide Calderazzo, Angelica Profiti, Federica Piedepalumbo, Francesco Blasi

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Elexacaftor/Tezacaftor/Ivacaftor Efficacy in a Cohort of Italian Patients with CFTR Rare Mutations by Francesca Lucca, Sonia Volpi, Mirco Ros, Benedetta Fabrizzi, Ilaria Meneghelli, Marica Bordicchia, Francesca Buniotto, Alessia Lancini, Cecilia Brignole, Francesca Pauro, Valentino Bezzerri, Marco Cipolli

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Development of translational read-through-inducing drugs as novel therapeutic options for patients with Fanconi anemia by Anca Manuela Hristodor, Enrico Cappelli, Elena Baldisseri, Roberto Valli, Giuseppe Montalbano, Giovanni Micheloni, Giovanni Porta, Annalisa Frattini, Silvia Ravera, Francesca Fioredda, Giuseppe Lippi, Carlo Dufour, Marco Cipolli, Valentino Bezzerri

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