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Clinical spectrum and uncommon features of McCune-Albright syndrome in children: a cohort study from a National Referral Center by Solène Bergignat, Roland Chapurlat, Roland Chapurlat, Roland Chapurlat, Marc Nicolino, Marc Nicolino, Kevin Perge, Kevin Perge
Published 2025-02-01Get full text
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O13: Oral infigratinib for children with achondroplasia: Month 18 results from the PROPEL 2 study by Ravi Savarirayan, Elena Muslimova, Josep Bergua, Paul Arundel, Jean Salles, Vrinda Saraff, Borja Delgado, Antonio Leiva-Gea, Helen McDevitt, Marc Nicolino, Massimiliano Rossi, Maria Salcedo, Valerie Cormier-Daire, Mars Skael, Peter Kannu, John Phillips, Howard Saal, Paul Harmatz, Toby Candler, Richard Weng, Yun Bai, Supriya Raj, Julie Hoover-Fong, Melita Irving, Daniela Rogoff
Published 2025-01-01Get full text
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