Spinal muscular atrophy in Brazil: from individual treatment to global management by Laurent Servais, Cristiane Araujo Martins Moreno

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Thrombotic Microangiopathy as an Emerging Complication of Viral Vector–Based Gene Therapy by Nora Schwotzer, Carine El Sissy, Isabelle Desguerre, Véronique Frémeaux-Bacchi, Laurent Servais, Fadi Fakhouri

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Why should a 5q spinal muscular atrophy neonatal screening program be started? by Michele Michelin Becker, Flávia Nardes, Tamara Dangouloff, Laurent Servais, Alexandra Prufer de Queiroz Campos Araujo, Juliana Gurgel-Giannetti

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A real-world analysis of the impact of X-linked myotubular myopathy on caregivers in the United States by Tina Duong, Tmirah Haselkorn, Beckley Miller, Julie Coats, Ivar Jensen, Erin Ward, Marie Wood, Robert J. Graham, Laurent Servais

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Newborn screening for spinal muscular atrophy in Ukraine: from pilot project to national programme by Nataliia Olkhovych, Nataliia Samonenko, Tetiana Shkliarska, Serena Hill, Olena Grechanina, Mykola Veropotvelyan, Halyna Makukh, Oksana Barvinska, Nataliia Mytsyk, Tamara Dangouloff, Tetiana Ivanova, Laurent Servais, Nataliia Gorovenko

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