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Generation of a cellular model for mucopolysaccharidosis type IVA (MPS IVA) (AOUMEYi003-A) from a patient carrying compound heterozygous mutations p.G116V and p.G290S in the GALNS... by Federica Feo, Silvia Falliano, Anna Caciotti, Marina Rinaldi, Alessia Caroli, Laura Giunti, Martino Calamai, Elena Procopio, Renzo Guerrini, Amelia Morrone, Rodolfo Tonin
Published 2025-09-01Get full text
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Gemcitabine–oxaliplatin as a bridge therapy toward autologous hematopoietic stem cell transplantation in infant-type brain tumors by Barbara Castelli, Carla Fonte, Marco Tellini, Marco Di Nicola, Milena Guidi, Laura Giunti, Bianca Tirinnanzi, Chiara Marzano, Anna Maria Buccoliero, Ludovico D’Incerti, Flavio Giordano, Mirko Scagnet, Veronica Tintori, Lorenzo Genitori, Iacopo Sardi
Published 2025-05-01Get full text
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