P019: Comparison of treatment efficacy of very long chain acyl-CoA (VLCAD) deficiency with an AAV9.hVLCAD vector, synthetic VLCAD mRNA, and triheptanoin by Jerry Vockley, Shakuntala Basu, Xue-Jun Zhao, Bianca Seminotti, Clinton Van't Land, Al-Walid Mohsen

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P049: The long-chain fatty acid oxidation disorders (LC-FAOD) disease monitoring program: An evaluation of initial findings by Jerry Vockley, Barbara Burton, Amarilis Sanchez Valle, Michal Inbar-Feigenberg, Anjali Aggarwal, Joel Hetzer, Bridget Reineking, Andrew Grimm

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Body‐Wide Inactivation of the Myc‐Like Mlx Transcription Factor Network Accelerates Aging and Increases the Lifetime Cancer Incidence by Huabo Wang, Taylor Stevens, Jie Lu, Alexander Roberts, Clinton Van't Land, Radhika Muzumdar, Zhenwei Gong, Jerry Vockley, Edward V. Prochownik

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P020: Introducing an interactive, searchable database of LC-FAOD gene variants, genotypes and phenotypes by Vanessa Rangel Miller, Omid Japalaghi, Heather Richbourg, Moeenaldeen AlSayed, Peter Baker, II, Sarah C. Grünert, Sean Daugherty, Tali Ekstein, Mark Kiel, Aneal Khan, Hironori Kobayashi, Lawrence Korngut, Stephanie Monteleone, Ida Vanessa Schwartz, Nicole Miller, Jerry Vockley

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Genotype-specific effects of elamipretide in patients with primary mitochondrial myopathy: a post hoc analysis of the MMPOWER-3 trial by Amel Karaa, Enrico Bertini, Valerio Carelli, Bruce Cohen, Gregory M. Ennes, Marni J. Falk, Amy Goldstein, Gráinne Gorman, Richard Haas, Michio Hirano, Thomas Klopstock, Mary Kay Koenig, Cornelia Kornblum, Costanza Lamperti, Anna Lehman, Nicola Longo, Maria Judit Molnar, Sumit Parikh, Han Phan, Robert D. S. Pitceathly, Russekk Saneto, Fernando Scaglia, Serenella Servidei, Mark Tarnopolsky, Antonio Toscano, Johan L. K. Van Hove, John Vissing, Jerry Vockley, Jeffrey S. Finman, Anthony Abbruscato, David A. Brown, Alana Sullivan, James A. Shiffer, Michelango Mancuso, on behalf of the MMPOWER-3 Trial Investigators

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