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Efficacy, safety, and quality of life 4 years after valoctocogene roxaparvovec gene transfer for severe hemophilia A in the phase 3 GENEr8-1 trial by Andrew D. Leavitt, Johnny Mahlangu, Priyanka Raheja, Emily Symington, Doris V. Quon, Adam Giermasz, Maria Fernanda López Fernández, Gili Kenet, Gillian Lowe, Nigel S. Key, Carolyn M. Millar, Steven W. Pipe, Bella Madan, Sheng-Chieh Chou, Robert Klamroth, Jane Mason, Hervé Chambost, Flora Peyvandi, Elaine Majerus, Dominic Pepperell, Christine Rivat, Hua Yu, Tara M. Robinson, Margareth C. Ozelo
Published 2024-11-01Get full text
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Malignant Mesenchymal Tumors of the Breast: Current Challenges and New Perspectives on Primary Sarcomas and Malignant Phyllodes Tumors by Flavia De Lauretis, Alejandro Martin Sanchez, Cristina Accetta, Beatrice Carnassale, Sabatino D’Archi, Alba Di Leone, Antonio Franco, Federica Gagliardi, Stefano Magno, Elena Jane Mason, Francesca Moschella, Lorenzo Scardina, Marta Silenzi, Angela Bucaro, Chiara V. Pirrottina, Nicoletta D’Alessandris, Antonino Mulè, Angela Santoro, Fabio Marazzi, Valeria Masiello, Alessandra Fabi, Armando Orlandi, Antonella Palazzo, Ida Paris, Maria Pia Foschini, Riccardo Masetti, Gianluca Franceschini
Published 2025-04-01Get full text
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