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Efficacy and safety of avalglucosidase alfa in Japanese patients with late-onset and infantile-onset Pompe diseases: A case series from clinical trials by Madoka Mori-Yoshimura, Hirotaka Ohki, Hideaki Mashimo, Kenji Inoue, Satoko Kumada, Takashi Kiyono, Akihiro Arimori, Mitsunobu Ikeda, Hirofumi Komaki
Published 2025-03-01Get full text
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