Safety and efficacy of leriglitazone in childhood cerebral adrenoleukodystrophy (NEXUS): an interim analysis of an open-label, phase 2/3 trialResearch in context by Ángeles García-Cazorla, Caroline Sevin, Juliana Ribeiro Constante, Elise Yazbeck, Hendrik Rosewich, Sandra Jimenez, Gloria Chia-Yi Chiang, Otto Rapalino, Paul Caruso, Daniel Balentine, Karl G. Helmer, Seth Bennett, Marco Emanuele, Laura Rodriguez-Pascau, Pilar Pizcueta, Guillem Pina, Anna Vilà, Maria Rovira, Adriana Mantilla, Uwe Meya, Arun Mistry, María Pascual, Sílvia Pascual, Marc Martinell, Patricia L. Musolino, Eric Mallack

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