Advancing AAV technology: From capsid design to scalable manufacturing by Daniel Stone, Mario Mietzsch, Giuseppe Ronzitti

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Rescue of lysosomal acid lipase deficiency in mice by rAAV8 liver gene transfer by Marine Laurent, Rim Harb, Christine Jenny, Julie Oustelandt, Simon Jimenez, Jeremie Cosette, Francesca Landini, Aristide Ferrante, Guillaume Corre, Nemanja Vujic, Claudia Piccoli, Anais Brassier, Laetitia Van Wittenberghe, Giuseppe Ronzitti, Dagmar Kratky, Consiglia Pacelli, Mario Amendola

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AAV vectors trigger DNA damage response-dependent pro-inflammatory signalling in human iPSC-derived CNS models and mouse brain by Helena Costa-Verdera, Vasco Meneghini, Zachary Fitzpatrick, Monah Abou Alezz, Emily Fabyanic, Xin Huang, Yulia Dzhashiashvili, Avantika Ahiya, Elisabeth Mangiameli, Erika Valeri, Giovanni Crivicich, Silvia Piccolo, Ivan Cuccovillo, Roberta Caccia, Ying Kai Chan, Bérangère Bertin, Giuseppe Ronzitti, Esteban A. Engel, Ivan Merelli, Federico Mingozzi, Angela Gritti, Klaudia Kuranda, Anna Kajaste-Rudnitski

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